Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study).

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Title: Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study).
Authors: Madruga-Garrido, Marcos1 (AUTHOR), Vázquez-Costa, Juan F.2,3,4,5 (AUTHOR), Medina-Cantillo, Julita6 (AUTHOR), Brañas, María7 (AUTHOR), Cattinari, María G.8 (AUTHOR), de Lemus, Mencía8,9 (AUTHOR), Díaz-Abós, Paola7 (AUTHOR), Sánchez-Menéndez, Victoria7 (AUTHOR), Terrancle, Ángeles7 (AUTHOR), Rebollo, Pablo10 (AUTHOR), Maurino, Jorge7 (AUTHOR) jorge.maurino@roche.com
Source: Neurology & Therapy. Jun2021, Vol. 10 Issue 1, p361-373. 13p.
Database: Academic Search Ultimate
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        Value: 10.1007/s40120-020-00229-w
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              Text: Jun2021
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