Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study).
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| Title: | Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study). |
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| Authors: | Madruga-Garrido, Marcos1 (AUTHOR), Vázquez-Costa, Juan F.2,3,4,5 (AUTHOR), Medina-Cantillo, Julita6 (AUTHOR), Brañas, María7 (AUTHOR), Cattinari, María G.8 (AUTHOR), de Lemus, Mencía8,9 (AUTHOR), Díaz-Abós, Paola7 (AUTHOR), Sánchez-Menéndez, Victoria7 (AUTHOR), Terrancle, Ángeles7 (AUTHOR), Rebollo, Pablo10 (AUTHOR), Maurino, Jorge7 (AUTHOR) jorge.maurino@roche.com |
| Source: | Neurology & Therapy. Jun2021, Vol. 10 Issue 1, p361-373. 13p. |
| Database: | Academic Search Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 150429711 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study). – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Madruga-Garrido%2C+Marcos%22">Madruga-Garrido, Marcos</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Vázquez-Costa%2C+Juan+F%2E%22">Vázquez-Costa, Juan F.</searchLink><relatesTo>2,3,4,5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Medina-Cantillo%2C+Julita%22">Medina-Cantillo, Julita</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Brañas%2C+María%22">Brañas, María</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Cattinari%2C+María+G%2E%22">Cattinari, María G.</searchLink><relatesTo>8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22de+Lemus%2C+Mencía%22">de Lemus, Mencía</searchLink><relatesTo>8,9</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Díaz-Abós%2C+Paola%22">Díaz-Abós, Paola</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sánchez-Menéndez%2C+Victoria%22">Sánchez-Menéndez, Victoria</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Terrancle%2C+Ángeles%22">Terrancle, Ángeles</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Rebollo%2C+Pablo%22">Rebollo, Pablo</searchLink><relatesTo>10</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Maurino%2C+Jorge%22">Maurino, Jorge</searchLink><relatesTo>7</relatesTo> (AUTHOR)<i> jorge.maurino@roche.com</i> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Neurology+%26+Therapy%22">Neurology & Therapy</searchLink>. Jun2021, Vol. 10 Issue 1, p361-373. 13p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=150429711 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1007/s40120-020-00229-w Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 13 StartPage: 361 Titles: – TitleFull: Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study). Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Madruga-Garrido, Marcos – PersonEntity: Name: NameFull: Vázquez-Costa, Juan F. – PersonEntity: Name: NameFull: Medina-Cantillo, Julita – PersonEntity: Name: NameFull: Brañas, María – PersonEntity: Name: NameFull: Cattinari, María G. – PersonEntity: Name: NameFull: de Lemus, Mencía – PersonEntity: Name: NameFull: Díaz-Abós, Paola – PersonEntity: Name: NameFull: Sánchez-Menéndez, Victoria – PersonEntity: Name: NameFull: Terrancle, Ángeles – PersonEntity: Name: NameFull: Rebollo, Pablo – PersonEntity: Name: NameFull: Maurino, Jorge IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 06 Text: Jun2021 Type: published Y: 2021 Identifiers: – Type: issn-print Value: 21938253 Numbering: – Type: volume Value: 10 – Type: issue Value: 1 Titles: – TitleFull: Neurology & Therapy Type: main |
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