Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study. - Vázquez-Costa, Juan F.; Branas-Pampillón, María; Medina-Cantillo, Julita; Povedano, Mónica; Pitarch-Castellano, Inmaculada; López-Lobato, Mercedes; Fernández-Ramos, Joaquín A.; Lafuente-Hidalgo, Miguel; Rojas-García, Ricard; Caballero-Caballero, José M.; Málaga, Ignacio; Eirís-Puñal, Jesús; et al. (Neurology & Therapy, 2023)