A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease.

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Title: A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease.
Authors: Ren, Hong1 (AUTHOR), Zhang, Wei2,3 (AUTHOR), Ouyang, Yan1 (AUTHOR), Guo, Junhong3 (AUTHOR), Xu, Hong4 (AUTHOR), Ma, Jie5 (AUTHOR), Luo, Xiaoping6 (AUTHOR), Pan, Xiaoxia1 (AUTHOR), Yuan, Yun2 (AUTHOR), Shen, Qian4 (AUTHOR), Li, Bin7 (AUTHOR), Feng, Qiqi7 (AUTHOR), Liu, Shi7 (AUTHOR), Chen, Nan1 (AUTHOR) cnrj100@126.com
Source: Orphanet Journal of Rare Diseases. 8/4/2025, Vol. 20 Issue 1, p1-12. 12p.
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  Data: A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease.
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 8/4/2025, Vol. 20 Issue 1, p1-12. 12p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=187118366
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      – Type: doi
        Value: 10.1186/s13023-025-03950-7
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        Text: English
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        PageCount: 12
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      – TitleFull: A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease.
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            – D: 04
              M: 08
              Text: 8/4/2025
              Type: published
              Y: 2025
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