A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease.
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| Title: | A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease. |
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| Authors: | Ren, Hong1 (AUTHOR), Zhang, Wei2,3 (AUTHOR), Ouyang, Yan1 (AUTHOR), Guo, Junhong3 (AUTHOR), Xu, Hong4 (AUTHOR), Ma, Jie5 (AUTHOR), Luo, Xiaoping6 (AUTHOR), Pan, Xiaoxia1 (AUTHOR), Yuan, Yun2 (AUTHOR), Shen, Qian4 (AUTHOR), Li, Bin7 (AUTHOR), Feng, Qiqi7 (AUTHOR), Liu, Shi7 (AUTHOR), Chen, Nan1 (AUTHOR) cnrj100@126.com |
| Source: | Orphanet Journal of Rare Diseases. 8/4/2025, Vol. 20 Issue 1, p1-12. 12p. |
| Database: | Academic Search Ultimate |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 187118366 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=187118366 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1186/s13023-025-03950-7 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 12 StartPage: 1 Titles: – TitleFull: A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Ren, Hong – PersonEntity: Name: NameFull: Zhang, Wei – PersonEntity: Name: NameFull: Ouyang, Yan – PersonEntity: Name: NameFull: Guo, Junhong – PersonEntity: Name: NameFull: Xu, Hong – PersonEntity: Name: NameFull: Ma, Jie – PersonEntity: Name: NameFull: Luo, Xiaoping – PersonEntity: Name: NameFull: Pan, Xiaoxia – PersonEntity: Name: NameFull: Yuan, Yun – PersonEntity: Name: NameFull: Shen, Qian – PersonEntity: Name: NameFull: Li, Bin – PersonEntity: Name: NameFull: Feng, Qiqi – PersonEntity: Name: NameFull: Liu, Shi – PersonEntity: Name: NameFull: Chen, Nan IsPartOfRelationships: – BibEntity: Dates: – D: 04 M: 08 Text: 8/4/2025 Type: published Y: 2025 Identifiers: – Type: issn-print Value: 17501172 Numbering: – Type: volume Value: 20 – Type: issue Value: 1 Titles: – TitleFull: Orphanet Journal of Rare Diseases Type: main |
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