Adherence, Persistence, and Safety of Risdiplam in Spinal Muscular Atrophy: A Population-Based Cohort Study.
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| Title: | Adherence, Persistence, and Safety of Risdiplam in Spinal Muscular Atrophy: A Population-Based Cohort Study. |
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| Authors: | Chovi-Trull, Maria1 (AUTHOR) mariach22ch@gmail.com, Ñungo-Garzón, Nancy C.2,3 (AUTHOR) carolina_nungo@iislafe.es, Aragon-Gawinska, Karolina A.2 (AUTHOR) karolina_gawinska@iislafe.es, Pitarch-Castellano, Inmaculada2,3,4,5 (AUTHOR) pitarch_inmcas@gva.es, Albert-Marí, Asunción1 (AUTHOR) albert_asu@gva.es, García-Pellicer, Javier1 (AUTHOR) garcia_javpel@gva.es, Poveda-Andrés, José L.6 (AUTHOR) poveda_josand@gva.es, Edo-Solsona, María D.1 (AUTHOR) edo_marsol@gva.es, Vázquez-Costa, Juan F.2,3,4,7 (AUTHOR) juan.vazquez@uv.es |
| Source: | Neurology & Therapy. May2026, p1-15. 15p. |
| Database: | Academic Search Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 193519273 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=193519273 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1007/s40120-026-00947-7 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 15 StartPage: 1 Titles: – TitleFull: Adherence, Persistence, and Safety of Risdiplam in Spinal Muscular Atrophy: A Population-Based Cohort Study. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Chovi-Trull, Maria – PersonEntity: Name: NameFull: Ñungo-Garzón, Nancy C. – PersonEntity: Name: NameFull: Aragon-Gawinska, Karolina A. – PersonEntity: Name: NameFull: Pitarch-Castellano, Inmaculada – PersonEntity: Name: NameFull: Albert-Marí, Asunción – PersonEntity: Name: NameFull: García-Pellicer, Javier – PersonEntity: Name: NameFull: Poveda-Andrés, José L. – PersonEntity: Name: NameFull: Edo-Solsona, María D. – PersonEntity: Name: NameFull: Vázquez-Costa, Juan F. IsPartOfRelationships: – BibEntity: Dates: – D: 06 M: 05 Text: May2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 21938253 Titles: – TitleFull: Neurology & Therapy Type: main |
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