Treatment of dysferlinopathy with deflazacort: a double-blind, placebo-controlled clinical trial. - Walter, Maggie C.; Reilich, Peter; Thiele, Simone; Schessl, Joachim; Schreiber, Herbert; Reiners, Karlheinz; Kress, Wolfram; Müller-Reible, Clemens; Vorgerd, Matthias; Urban, Peter; Schrank, Bertold; Deschauer, Marcus; et al. (Orphanet Journal of Rare Diseases, 2013)