Cas-Based Systems for RNA Editing in Gene Therapy of Monogenic Diseases: In Vitro and in Vivo Application and Translational Potential.

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Title: Cas-Based Systems for RNA Editing in Gene Therapy of Monogenic Diseases: In Vitro and in Vivo Application and Translational Potential.
Authors: Reshetnikov VV; Department of Biotechnology, Sirius University of Science and Technology, Sochi, Russia.; Department of Molecular Genetics, Institute of Cytology and Genetics, Novosibirsk, Russia., Chirinskaite AV; Center of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia., Sopova JV; Center of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.; Laboratory of Amyloid Biology, St. Petersburg State University, St. Petersburg, Russia., Ivanov RA; Department of Biotechnology, Sirius University of Science and Technology, Sochi, Russia., Leonova EI; Center of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.; Scientific Center for Genetics and Life Sciences, Sirius University of Science and Technology, Sochi, Russia.
Source: Frontiers in cell and developmental biology [Front Cell Dev Biol] 2022 Jun 16; Vol. 10, pp. 903812. Date of Electronic Publication: 2022 Jun 16 (Print Publication: 2022).
Publication Type: Journal Article; Review
Journal Info: Publisher: Frontiers Media S.A Country of Publication: Switzerland NLM ID: 101630250 Publication Model: eCollection Cited Medium: Print ISSN: 2296-634X (Print) Linking ISSN: 2296634X NLM ISO Abbreviation: Front Cell Dev Biol Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: Cas-Based Systems for RNA Editing in Gene Therapy of Monogenic Diseases: In Vitro and in Vivo Application and Translational Potential.
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  Data: <searchLink fieldCode="AU" term="%22Reshetnikov+VV%22">Reshetnikov VV</searchLink>; Department of Biotechnology, Sirius University of Science and Technology, Sochi, Russia.; Department of Molecular Genetics, Institute of Cytology and Genetics, Novosibirsk, Russia.<br /><searchLink fieldCode="AU" term="%22Chirinskaite+AV%22">Chirinskaite AV</searchLink>; Center of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.<br /><searchLink fieldCode="AU" term="%22Sopova+JV%22">Sopova JV</searchLink>; Center of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.; Laboratory of Amyloid Biology, St. Petersburg State University, St. Petersburg, Russia.<br /><searchLink fieldCode="AU" term="%22Ivanov+RA%22">Ivanov RA</searchLink>; Department of Biotechnology, Sirius University of Science and Technology, Sochi, Russia.<br /><searchLink fieldCode="AU" term="%22Leonova+EI%22">Leonova EI</searchLink>; Center of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.; Scientific Center for Genetics and Life Sciences, Sirius University of Science and Technology, Sochi, Russia.
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  Data: <searchLink fieldCode="JN" term="%22101630250%22">Frontiers in cell and developmental biology</searchLink> [Front Cell Dev Biol] 2022 Jun 16; Vol. 10, pp. 903812. <i>Date of Electronic Publication: </i>2022 Jun 16 (<i>Print Publication: </i>2022).
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        Value: 10.3389/fcell.2022.903812
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              Text: 2022 Jun 16
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