The translational gap for gene therapies in low- and middle-income countries.
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| Title: | The translational gap for gene therapies in low- and middle-income countries. |
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| Authors: | Doxzen KW; Strategic Analysis Inc., Arlington, VA, USA., Adair JE; Translational Science and Therapeutics Division, Fred Hutchinson Cancer Center, Seattle, WA, USA.; Departments of Medical Oncology and Laboratory Medicine and Pathology, University of Washington, Seattle, WA, USA., Fonseca Bazzo YM; Department of Pharmaceutical Sciences, Faculty of Health Sciences, University of Brasília, Brasília, DF, Brazil., Bukini D; Sickle Cell Programme, Department of Haematology and Blood Transfusion, Muhimbili University of Health & Allied Sciences (MUHAS), Dar-es-Salaam, Tanzania.; SickleInAfrica Clinical Coordinating Center, Muhimbili University of Health & Allied Sciences (MUHAS), Dar-es-Salaam, Tanzania., Cornetta K; Indiana University School of Medicine, Indianapolis, IN, USA., Dalal V; Department of Health Research, Ministry of Health and Family Welfare, Government of India, New Delhi, India., Guerino-Cunha RL; Centro Paulista de Oncologia, Grupo Oncoclínicas, São Paulo, SP, Brazil.; Instituto Oncoclínicas, Rio de Janeiro, RJ, Brazil., Hongeng S; Division of Hematology and Oncology, Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok, Thailand., Jotwani G; Indian Council of Medical Research, New Delhi, India., Kityo-Mutuluuza C; Joint Clinical Research Centre (JCRC), Kampala, Uganda., Lakshmanan K; Department of Pediatric Hematology and Oncology, Yale School of Medicine, New Haven, CT, USA., Mahlangu J; Department of Molecular Medicine and Haematology, Faculty of Health Sciences, University of the Witwatersrand and NHLS, Johannesburg, South Africa., Makani J; Sickle Cell Programme, Department of Haematology and Blood Transfusion, Muhimbili University of Health & Allied Sciences (MUHAS), Dar-es-Salaam, Tanzania.; SickleInAfrica Clinical Coordinating Center, Muhimbili University of Health & Allied Sciences (MUHAS), Dar-es-Salaam, Tanzania.; Centre for Haematology, Department of Immunology and Inflammation, Imperial College London, London, UK., Mathews V; Department of Haematology, Christian Medical College (CMC), Vellore, India., Ozelo MC; INCT Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, SP, Brazil., Rangarajan S; Advanced Center for Oncology, Haematology & Rare Disorders (ACOHRD), K. J. Somaiya Medical College & Research Center, Somaiya Ayurvihar, Mumbai, Maharashtra, India.; Faculty of Medicine, University of Southampton, Southampton, UK., Scholefield J; Bioengineering and Integrated Genomics Group, Next Generation Health Cluster, Council for Scientific and Industrial Research, Pretoria, South Africa.; Department of Human Biology, Faculty of Health Sciences, University of Cape Town, Cape Town, South Africa., Batista Silva Júnior J; Brazilian Health Regulatory Agency-ANVISA, Brasília, DF, Brazil.; Department of Pharmaceutical Sciences, Faculty of Health Sciences, University of Brasília, Brasília, DF, Brazil., McCune JM; HIV Frontiers, Global Health Accelerator, Bill & Melinda Gates Foundation, Seattle, WA, USA. |
| Source: | Science translational medicine [Sci Transl Med] 2024 May 08; Vol. 16 (746), pp. eadn1902. Date of Electronic Publication: 2024 May 08. |
| Publication Type: | Journal Article; Review; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: American Association for the Advancement of Science Country of Publication: United States NLM ID: 101505086 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1946-6242 (Electronic) Linking ISSN: 19466234 NLM ISO Abbreviation: Sci Transl Med Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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