ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma.

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Title: ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma.
Authors: Moertel CL; Department of Pediatrics, University of Minnesota, Minneapolis, MN., Hirbe AC; Washington University School of Medicine in St Louis, St Louis, MO., Shuhaiber HH; University of Florida Clinical Research Center, Gainesville, FL., Bielamowicz K; The University of Arkansas for Medical Sciences/Arkansas Children's Hospital, Little Rock, AR., Sidhu A; University of Iowa Hospitals and Clinics, Iowa City, IA., Viskochil D; University of Utah, Salt Lake City, UT., Weber MD; SpringWorks Therapeutics, Inc, Stamford, CT., Lokku A; SpringWorks Therapeutics, Inc, Stamford, CT., Smith LM; SpringWorks Therapeutics, Inc, Stamford, CT., Foreman NK; Children's Hospital Colorado, Aurora, CO., Hajjar FM; AdventHealth for Children, Orlando, FL., McNall-Knapp RY; University of Oklahoma Health Sciences Center, Oklahoma City, OK., Weintraub L; Albany Medical Center, Albany, NY., Antony R; University of California Davis, Sacramento, CA., Franson AT; University of Michigan, Ann Arbor, MI., Meade J; University of Pittsburgh School of Medicine, Pittsburgh, PA., Schiff D; University of Virginia Medical Center, Charlottesville, VA., Walbert T; Henry Ford Health, Wayne State University and Michigan State University, Detroit, MI., Ambady P; Oregon Health and Science University, Portland, OR., Bota DA; University of California, Irvine, CA., Campen CJ; Stanford/Lucile Packard Children's Hospital and Stanford Children's Health, Palo Alto, CA., Kaur G; New York Presbyterian Morgan Stanley Children's Hospital, Columbia University Medical Center, New York, NY., Klesse LJ; University of Texas Southwestern/Children's Health, Dallas, TX., Maraka S; University of Illinois at Chicago, Chicago, IL., Moots PL; Vanderbilt University Medical Center/Vanderbilt-Ingram Cancer Center, Nashville, TN., Nevel K; Indiana University Health/Indiana University School of Medicine, Indianapolis, IL., Bornhorst M; Children's National Hospital, Washington, DC., Aguilar-Bonilla A; Orlando Health, Inc, Orlando, FL., Chagnon S; Children's Hospital of the Kings Daughters, Norfolk, VA., Dalvi N; Montefiore Medical Center/Children's Hospital at Montefiore, New York City, NY., Gupta P; St Joseph's Regional Medical Center, Paterson, NJ., Khatib Z; Nicklaus Children's Hospital, Miami, FL., Metrock LK; University of Alabama at Birmingham, Birmingham, AL., Nghiemphu PL; University of California, Los Angeles (UCLA), Los Angeles, CA., Roberts RD; Nationwide Children's Hospital, Columbus, OH., Robison NJ; Children's Hospital Los Angeles, Los Angeles, CA., Sadighi Z; University of Texas MD Anderson Cancer Center, Houston, TX., Stapleton S; Johns Hopkins All Children's Hospital, St Petersburg, FL., Babovic-Vuksanovic D; Mayo Clinic, Rochester, MN., Gershon TR; Department of Pediatrics, Emory University, Atlanta, GA.
Corporate Authors: ReNeu Trial Investigators, ReNeu Study Investigators
Source: Journal of clinical oncology : official journal of the American Society of Clinical Oncology [J Clin Oncol] 2025 Feb 20; Vol. 43 (6), pp. 716-729. Date of Electronic Publication: 2024 Nov 08.
Publication Type: Journal Article; Clinical Trial, Phase II; Multicenter Study; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
Journal Info: Publisher: American Society of Clinical Oncology Country of Publication: United States NLM ID: 8309333 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1527-7755 (Electronic) Linking ISSN: 0732183X NLM ISO Abbreviation: J Clin Oncol Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1527-7755
DOI:10.1200/JCO.24.01034