View in EDS HTML Full Text PDF Full Text

A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.

Saved in:
Bibliographic Details
Title: A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.
Authors: Wilk J; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.; Department of Mathematics, College of Sciences, University of Central Florida, Orlando, Florida, USA., Aggarwal V; Critical Path Institute (C-Path), Tucson, Arizona, USA., Pauley M; Critical Path Institute (C-Path), Tucson, Arizona, USA., Corey D; Critical Path Institute (C-Path), Tucson, Arizona, USA., Conrado DJ; e-Quantify LLC, La Jolla, California, USA., Lingineni K; Novartis Pharmaceutical Corporation, Cambridge, Massachusetts, USA., Morales JF; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.; Critical Path Institute (C-Path), Tucson, Arizona, USA., Yoon DY; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA., Zhang Y; Critical Path Institute (C-Path), Tucson, Arizona, USA., Cui Z; Critical Path Institute (C-Path), Tucson, Arizona, USA., Burton J; Biogen, Cambridge, Massachusetts, USA., Larkindale J; Critical Path Institute (C-Path), Tucson, Arizona, USA., Ma SC; Critical Path Institute (C-Path), Tucson, Arizona, USA., Hovinga C; Critical Path Institute (C-Path), Tucson, Arizona, USA., Martinez T; Critical Path Institute (C-Path), Tucson, Arizona, USA., Romero K; Critical Path Institute (C-Path), Tucson, Arizona, USA., Belfiore-Oshan R; Critical Path Institute (C-Path), Tucson, Arizona, USA., Kim S; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.
Corporate Authors: Duchenne Regulatory Science Consortium (D‐RSC) and the CINRG DNHS investigators
Source: CPT: pharmacometrics & systems pharmacology [CPT Pharmacometrics Syst Pharmacol] 2025 Nov; Vol. 14 (11), pp. 1787-1796. Date of Electronic Publication: 2024 Nov 27.
Publication Type: Case Reports; Journal Article
Journal Info: Publisher: Wiley Country of Publication: United States NLM ID: 101580011 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2163-8306 (Electronic) Linking ISSN: 21638306 NLM ISO Abbreviation: CPT Pharmacometrics Syst Pharmacol Subsets: MEDLINE
Database: MEDLINE Ultimate
Full text is not displayed to guests.
FullText Links:
  – Type: pdflink
Text:
  Availability: 1
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 39600251
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Wilk+J%22">Wilk J</searchLink>; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.; Department of Mathematics, College of Sciences, University of Central Florida, Orlando, Florida, USA.<br /><searchLink fieldCode="AU" term="%22Aggarwal+V%22">Aggarwal V</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Pauley+M%22">Pauley M</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Corey+D%22">Corey D</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Conrado+DJ%22">Conrado DJ</searchLink>; e-Quantify LLC, La Jolla, California, USA.<br /><searchLink fieldCode="AU" term="%22Lingineni+K%22">Lingineni K</searchLink>; Novartis Pharmaceutical Corporation, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Morales+JF%22">Morales JF</searchLink>; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Yoon+DY%22">Yoon DY</searchLink>; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.<br /><searchLink fieldCode="AU" term="%22Zhang+Y%22">Zhang Y</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Cui+Z%22">Cui Z</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Burton+J%22">Burton J</searchLink>; Biogen, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Larkindale+J%22">Larkindale J</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Ma+SC%22">Ma SC</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Hovinga+C%22">Hovinga C</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Martinez+T%22">Martinez T</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Romero+K%22">Romero K</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Belfiore-Oshan+R%22">Belfiore-Oshan R</searchLink>; Critical Path Institute (C-Path), Tucson, Arizona, USA.<br /><searchLink fieldCode="AU" term="%22Kim+S%22">Kim S</searchLink>; Department of Pharmaceutics, Center for Pharmacometrics and Systems Pharmacology, College of Pharmacy, University of Florida, Orlando, Florida, USA.
– Name: AuthorCorporate
  Label: Corporate Authors
  Group: Au
  Data: <searchLink fieldCode="CA" term="%22Duchenne+Regulatory+Science+Consortium+%28D‐RSC%29+and+the+CINRG+DNHS+investigators%22">Duchenne Regulatory Science Consortium (D‐RSC) and the CINRG DNHS investigators</searchLink>
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22101580011%22">CPT: pharmacometrics & systems pharmacology</searchLink> [CPT Pharmacometrics Syst Pharmacol] 2025 Nov; Vol. 14 (11), pp. 1787-1796. <i>Date of Electronic Publication: </i>2024 Nov 27.
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Case Reports; Journal Article
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Wiley%22">Wiley </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101580011 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2163-8306 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2221638306%22">21638306 </searchLink><i>NLM ISO Abbreviation: </i>CPT Pharmacometrics Syst Pharmacol <i>Subsets: </i>MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=39600251
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1002/psp4.13281
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        StartPage: 1787
    Titles:
      – TitleFull: A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Wilk J
      – PersonEntity:
          Name:
            NameFull: Aggarwal V
      – PersonEntity:
          Name:
            NameFull: Pauley M
      – PersonEntity:
          Name:
            NameFull: Corey D
      – PersonEntity:
          Name:
            NameFull: Conrado DJ
      – PersonEntity:
          Name:
            NameFull: Lingineni K
      – PersonEntity:
          Name:
            NameFull: Morales JF
      – PersonEntity:
          Name:
            NameFull: Yoon DY
      – PersonEntity:
          Name:
            NameFull: Zhang Y
      – PersonEntity:
          Name:
            NameFull: Cui Z
      – PersonEntity:
          Name:
            NameFull: Burton J
      – PersonEntity:
          Name:
            NameFull: Larkindale J
      – PersonEntity:
          Name:
            NameFull: Ma SC
      – PersonEntity:
          Name:
            NameFull: Hovinga C
      – PersonEntity:
          Name:
            NameFull: Martinez T
      – PersonEntity:
          Name:
            NameFull: Romero K
      – PersonEntity:
          Name:
            NameFull: Belfiore-Oshan R
      – PersonEntity:
          Name:
            NameFull: Kim S
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 01
              M: 11
              Text: 2025 Nov
              Type: published
              Y: 2025
          Identifiers:
            – Type: issn-electronic
              Value: 2163-8306
          Numbering:
            – Type: volume
              Value: 14
            – Type: issue
              Value: 11
          Titles:
            – TitleFull: CPT: pharmacometrics & systems pharmacology
              Type: main
ResultId 1