Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases-A secondary analysis of a randomized clinical trial.

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Title: Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases-A secondary analysis of a randomized clinical trial.
Authors: Wied S; Institute of Medical Statistics, RWTH Aachen University, Aachen, Germany., Hilgers RD; Institute of Medical Statistics, RWTH Aachen University, Aachen, Germany., Heussen N; Institute of Medical Statistics, RWTH Aachen University, Aachen, Germany.; Medical School, Sigmund Freud Private University, Vienna, Austria., Kotulska K; Department of Neurology and Epileptology, The Children's Memorial Health Insitute, Member of Epicare, Warsaw, Poland., Dirani M; Department of Pediatric Neurology, Imagine Institute Paris, Necker-Enfants Maelades Hospital, Reference Centre for Rare Epilepsies, Member of Epicare, University Paris cite, Paris, France., Kuchenbuch M; Department of Pediatric Neurology, Imagine Institute Paris, Necker-Enfants Maelades Hospital, Reference Centre for Rare Epilepsies, Member of Epicare, University Paris cite, Paris, France., Jozwiak S; Research Department, The Children's Memorial Health Insitute, Member of Epicare, Warsaw, Poland., Nabbout R; Department of Pediatric Neurology, Imagine Institute Paris, Necker-Enfants Maelades Hospital, Reference Centre for Rare Epilepsies, Member of Epicare, University Paris cite, Paris, France.
Source: PloS one [PLoS One] 2024 Dec 03; Vol. 19 (12), pp. e0312936. Date of Electronic Publication: 2024 Dec 03 (Print Publication: 2024).
Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial
Journal Info: Publisher: Public Library of Science Country of Publication: United States NLM ID: 101285081 Publication Model: eCollection Cited Medium: Internet ISSN: 1932-6203 (Electronic) Linking ISSN: 19326203 NLM ISO Abbreviation: PLoS One Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases-A secondary analysis of a randomized clinical trial.
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  Data: <searchLink fieldCode="AU" term="%22Wied+S%22">Wied S</searchLink>; Institute of Medical Statistics, RWTH Aachen University, Aachen, Germany.<br /><searchLink fieldCode="AU" term="%22Hilgers+RD%22">Hilgers RD</searchLink>; Institute of Medical Statistics, RWTH Aachen University, Aachen, Germany.<br /><searchLink fieldCode="AU" term="%22Heussen+N%22">Heussen N</searchLink>; Institute of Medical Statistics, RWTH Aachen University, Aachen, Germany.; Medical School, Sigmund Freud Private University, Vienna, Austria.<br /><searchLink fieldCode="AU" term="%22Kotulska+K%22">Kotulska K</searchLink>; Department of Neurology and Epileptology, The Children's Memorial Health Insitute, Member of Epicare, Warsaw, Poland.<br /><searchLink fieldCode="AU" term="%22Dirani+M%22">Dirani M</searchLink>; Department of Pediatric Neurology, Imagine Institute Paris, Necker-Enfants Maelades Hospital, Reference Centre for Rare Epilepsies, Member of Epicare, University Paris cite, Paris, France.<br /><searchLink fieldCode="AU" term="%22Kuchenbuch+M%22">Kuchenbuch M</searchLink>; Department of Pediatric Neurology, Imagine Institute Paris, Necker-Enfants Maelades Hospital, Reference Centre for Rare Epilepsies, Member of Epicare, University Paris cite, Paris, France.<br /><searchLink fieldCode="AU" term="%22Jozwiak+S%22">Jozwiak S</searchLink>; Research Department, The Children's Memorial Health Insitute, Member of Epicare, Warsaw, Poland.<br /><searchLink fieldCode="AU" term="%22Nabbout+R%22">Nabbout R</searchLink>; Department of Pediatric Neurology, Imagine Institute Paris, Necker-Enfants Maelades Hospital, Reference Centre for Rare Epilepsies, Member of Epicare, University Paris cite, Paris, France.
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