Multi-stakeholder sessions on major innovation topics in rare disease clinical trials.

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Bibliographic Details
Title: Multi-stakeholder sessions on major innovation topics in rare disease clinical trials.
Authors: Bodden D; Institute of Medical Statistics, RWTH Aachen University Aachen, Pauwelsstrasse 19, 52064, Aachen, Germany. daniel.bodden@rwth-aachen.de., Schoenen S; Institute of Medical Statistics, RWTH Aachen University Aachen, Pauwelsstrasse 19, 52064, Aachen, Germany., Wied S; Institute of Medical Statistics, RWTH Aachen University Aachen, Pauwelsstrasse 19, 52064, Aachen, Germany., Verbeeck J; I-BioStat, Data Science Institute, Hasselt University, Martelarenlaan 42, 3500, Hasselt, Belgium., Dirani M; Institut des Maladies Gènètiques Imagine- Necker Enfants malades Hospital, 24 Boulevard du Montparnasse, 75015, Paris, France.; Necker Enfants malades Hospital, 149 Rue de Sèvre, 75015, Paris, France., Abou Daya H; Thematic Institute of Genetics, Genomics & Bioinformatics, INSERM, 8 rue de la Croix Jarry, 75013, Paris, France., Heussen N; Institute of Medical Statistics, RWTH Aachen University Aachen, Pauwelsstrasse 19, 52064, Aachen, Germany.; Medical School, Sigmund Freud Private University, Freudplatz 1, 1020, Vienna, Austria., Molenberghs G; I-BioStat, Data Science Institute, Hasselt University, Martelarenlaan 42, 3500, Hasselt, Belgium.; I-BioStat, KU Leuven, Kapucijnenvoer 35, 3000, Leuven, Belgium., Hilgers RD; Institute of Medical Statistics, RWTH Aachen University Aachen, Pauwelsstrasse 19, 52064, Aachen, Germany., Nabbout R; Institut des Maladies Gènètiques Imagine- Necker Enfants malades Hospital, 24 Boulevard du Montparnasse, 75015, Paris, France.; Necker Enfants malades Hospital, 149 Rue de Sèvre, 75015, Paris, France.
Source: Orphanet journal of rare diseases [Orphanet J Rare Dis] 2024 Dec 19; Vol. 19 (1), pp. 467. Date of Electronic Publication: 2024 Dec 19.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172 (Electronic) Linking ISSN: 17501172 NLM ISO Abbreviation: Orphanet J Rare Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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