Azacytidine Monotherapy in an Infant With Mosaic NRAS-Driven Juvenile Myelomonocytic Leukemia.

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Title: Azacytidine Monotherapy in an Infant With Mosaic NRAS-Driven Juvenile Myelomonocytic Leukemia.
Authors: Grenier JM; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA., Tasian SK; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.; Prinses Máxima Center for Pediatric Oncology, Utrecht, the Netherlands., Stieglitz E; Division of Hematology-Oncology, Department of Pediatrics, University of California, San Francisco Benioff Children's Hospital, San Francisco, California, USA., Abdullaev Z; National Cancer Institute, Center for Cancer Research, Laboratory of Pathology, Bethesda, Maryland, USA., Wertheim GB; Division of Hematopathology, Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA., Li MM; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.; Division of Genomic Diagnostics, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA., Phillips CA; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.
Source: Pediatric blood & cancer [Pediatr Blood Cancer] 2025 May; Vol. 72 (5), pp. e31647. Date of Electronic Publication: 2025 Mar 04.
Publication Type: Letter
Journal Info: Publisher: John Wiley Country of Publication: United States NLM ID: 101186624 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1545-5017 (Electronic) Linking ISSN: 15455009 NLM ISO Abbreviation: Pediatr Blood Cancer Subsets: MEDLINE; In Process
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  Data: Azacytidine Monotherapy in an Infant With Mosaic NRAS-Driven Juvenile Myelomonocytic Leukemia.
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  Data: <searchLink fieldCode="AU" term="%22Grenier+JM%22">Grenier JM</searchLink>; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Tasian+SK%22">Tasian SK</searchLink>; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.; Prinses Máxima Center for Pediatric Oncology, Utrecht, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Stieglitz+E%22">Stieglitz E</searchLink>; Division of Hematology-Oncology, Department of Pediatrics, University of California, San Francisco Benioff Children's Hospital, San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Abdullaev+Z%22">Abdullaev Z</searchLink>; National Cancer Institute, Center for Cancer Research, Laboratory of Pathology, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Wertheim+GB%22">Wertheim GB</searchLink>; Division of Hematopathology, Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Li+MM%22">Li MM</searchLink>; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.; Division of Genomic Diagnostics, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Phillips+CA%22">Phillips CA</searchLink>; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.
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  Data: <searchLink fieldCode="JN" term="%22101186624%22">Pediatric blood & cancer</searchLink> [Pediatr Blood Cancer] 2025 May; Vol. 72 (5), pp. e31647. <i>Date of Electronic Publication: </i>2025 Mar 04.
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      – TitleFull: Azacytidine Monotherapy in an Infant With Mosaic NRAS-Driven Juvenile Myelomonocytic Leukemia.
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