Therapeutic switch from plasma to recombinant ADAMTS13 for patients with congenital TTP from Japanese real-world data.

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Title: Therapeutic switch from plasma to recombinant ADAMTS13 for patients with congenital TTP from Japanese real-world data.
Authors: Sakai K; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan., Hamamura A; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan., Yoshimura Y; Department of Pediatrics, Higashiosaka City Medical Center, Higashiosaka, Japan., Abe M; Department of Hematology, Oita Koseiren Tsurumi Hospital, Beppu, Japan., Ogawa Y; Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan., Tanaka K; Department of Nephrology, Aichi Children's Health and Medical Center, Obu, Japan., Hattori N; Division of Hematology, Department of Medicine, Showa University School of Medicine, Tokyo, Japan., Tokugawa T; Department of Hematology, Hyogo Medical University Hospital, Nishinomiya, Japan., Kanai R; Department of Pediatrics, Shimane Prefectural Central Hospital, Izumo, Japan., Ikejiri F; Department of Internal Medicine, Okuizumo Town Hospital, Okuizumo, Japan., Takeyama M; Division of Hemophilia, National Hospital Organization, Osaka National Hospital, Osaka, Japan., Taoka T; Department of Hematology, Sakaide City Hospital, Sakaide, Japan., Fujita N; Department of Diabetes/Endocrinology/Hematology, Saiseikai Yamaguchi General Hospital, Yamaguchi, Japan., Kanaya M; Blood Disorders Center, Aiiku Hospital, Sapporo, Japan., Koh K; Department of Hematology/Oncology, Saitama Children's Medical Center, Saitama, Japan., Shiragami H; Department of Hematology, Izumiotsu Medical Center, Izumi, Japan., Azumi H; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan., Saito K; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan., Matsumoto M; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan.; Department of Hematology, Nara Medical University, Kashihara, Japan.
Source: Blood [Blood] 2025 May 15; Vol. 145 (20), pp. 2390-2395.
Publication Type: Journal Article
Journal Info: Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Therapeutic switch from plasma to recombinant ADAMTS13 for patients with congenital TTP from Japanese real-world data.
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  Data: <searchLink fieldCode="AU" term="%22Sakai+K%22">Sakai K</searchLink>; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan.<br /><searchLink fieldCode="AU" term="%22Hamamura+A%22">Hamamura A</searchLink>; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan.<br /><searchLink fieldCode="AU" term="%22Yoshimura+Y%22">Yoshimura Y</searchLink>; Department of Pediatrics, Higashiosaka City Medical Center, Higashiosaka, Japan.<br /><searchLink fieldCode="AU" term="%22Abe+M%22">Abe M</searchLink>; Department of Hematology, Oita Koseiren Tsurumi Hospital, Beppu, Japan.<br /><searchLink fieldCode="AU" term="%22Ogawa+Y%22">Ogawa Y</searchLink>; Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan.<br /><searchLink fieldCode="AU" term="%22Tanaka+K%22">Tanaka K</searchLink>; Department of Nephrology, Aichi Children's Health and Medical Center, Obu, Japan.<br /><searchLink fieldCode="AU" term="%22Hattori+N%22">Hattori N</searchLink>; Division of Hematology, Department of Medicine, Showa University School of Medicine, Tokyo, Japan.<br /><searchLink fieldCode="AU" term="%22Tokugawa+T%22">Tokugawa T</searchLink>; Department of Hematology, Hyogo Medical University Hospital, Nishinomiya, Japan.<br /><searchLink fieldCode="AU" term="%22Kanai+R%22">Kanai R</searchLink>; Department of Pediatrics, Shimane Prefectural Central Hospital, Izumo, Japan.<br /><searchLink fieldCode="AU" term="%22Ikejiri+F%22">Ikejiri F</searchLink>; Department of Internal Medicine, Okuizumo Town Hospital, Okuizumo, Japan.<br /><searchLink fieldCode="AU" term="%22Takeyama+M%22">Takeyama M</searchLink>; Division of Hemophilia, National Hospital Organization, Osaka National Hospital, Osaka, Japan.<br /><searchLink fieldCode="AU" term="%22Taoka+T%22">Taoka T</searchLink>; Department of Hematology, Sakaide City Hospital, Sakaide, Japan.<br /><searchLink fieldCode="AU" term="%22Fujita+N%22">Fujita N</searchLink>; Department of Diabetes/Endocrinology/Hematology, Saiseikai Yamaguchi General Hospital, Yamaguchi, Japan.<br /><searchLink fieldCode="AU" term="%22Kanaya+M%22">Kanaya M</searchLink>; Blood Disorders Center, Aiiku Hospital, Sapporo, Japan.<br /><searchLink fieldCode="AU" term="%22Koh+K%22">Koh K</searchLink>; Department of Hematology/Oncology, Saitama Children's Medical Center, Saitama, Japan.<br /><searchLink fieldCode="AU" term="%22Shiragami+H%22">Shiragami H</searchLink>; Department of Hematology, Izumiotsu Medical Center, Izumi, Japan.<br /><searchLink fieldCode="AU" term="%22Azumi+H%22">Azumi H</searchLink>; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan.<br /><searchLink fieldCode="AU" term="%22Saito+K%22">Saito K</searchLink>; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan.<br /><searchLink fieldCode="AU" term="%22Matsumoto+M%22">Matsumoto M</searchLink>; Department of Blood Transfusion Medicine, Nara Medical University, Kashihara, Japan.; Department of Hematology, Nara Medical University, Kashihara, Japan.
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  Data: <searchLink fieldCode="JN" term="%227603509%22">Blood</searchLink> [Blood] 2025 May 15; Vol. 145 (20), pp. 2390-2395.
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              Text: 2025 May 15
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