Never-Treated, Non Splenectomised Patients With Gaucher Disease (The French GANT Study): The Prospective Follow-Up.

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Title: Never-Treated, Non Splenectomised Patients With Gaucher Disease (The French GANT Study): The Prospective Follow-Up.
Authors: Nasce A; Department of Endocrinology, Diabetes, Nutrition, Geneva University Hospitals, Geneva, Switzerland., Nguyen Y; Department of Internal Medicine, Reference Center for Lysosomal Diseases, AP-HP Nord, Paris Cité University, Beaujon Hospital, Paris, France.; Center for Epidemiology and Statistics, Université Paris Cité (CRESS), INSERM U1153, Paris, France., Belmatoug N; Department of Internal Medicine, Reference Center for Lysosomal Diseases, AP-HP Nord, Paris Cité University, Beaujon Hospital, Paris, France., Yousfi K; Department of Internal Medicine, Reference Center for Lysosomal Diseases, AP-HP Nord, Paris Cité University, Beaujon Hospital, Paris, France., Camou F; Department of Internal Medicine, Haut Lévêque Hospital, Bordeaux University Hospital, Pessac, France., Pettazzoni M; Biochemical and Molecular Biology Department, Centre de Biologie et de Pathologie Est, Hospices Civils de Lyon, Bron, France., Dalbies F; Institute of Cancerology and Hematology, CHRU Morvan, Brest, France., Cador B; Department of Internal Medicine, Pontchaillou University Hospital, Rennes, France., Brassier A; Reference Center for Inherited Metabolic Diseases, Necker-Enfants Malades Hospital, Paris, France., Pichard S; Reference Center for Inherited Metabolic Diseases, Necker-Enfants Malades Hospital, Paris, France., Hivert B; Department of Clinical Hematology, Hospital Saint Vincent de Paul, Lille, France., Swiader L; Department of Internal Medicine, Timone University Hospital, Marseille, France., Bertchansky I; Department of Internal Medicine, Saint-Eloi Hospital, University Hospital, Montpellier, France., Seguin VL; Department of Internal Medicine and Clinical Immunology, F. Mitterrand University Hospital, Dijon, France., Mauhin W; Department of Internal Medicine, La Croix Saint Simon Hospital, Paris, France., Astudillo L; Department of Internal Medicine, Saint Exupery Clinic, Toulouse, France., Rainsard IH; Department of General Pediatrics, CHI Creteil, Créteil, France., Humbert S; Hematology Department, University Hospital of Besançon, Besançon, France., Hoebeke C; Department of Pediatric Neurology, French Reference Center for Hereditary Metabolic Diseases, Hôpital Timone Enfants, Marseille, France., Hamroun D; Research and Innovation Department, University Hospital of Montpellier, Montpellier, France., Masseau A; Service de Médecine Interne, CHU Hôtel Dieu, Nantes, France., Berger MG; Hematology Department and EA 7453 CHELTER, Clermont Auvergne University and CHU Clermont-Ferrand, Clermont-Ferrand, France., Stirnemann J; Department of Internal Medicine, Department of Medicine, Geneva University Hospitals, Geneva, Switzerland., Serratrice C; Division of Internal Medicine of the Aged, Geneva University Hospitals, Geneva, Switzerland.
Corporate Authors: Comité d'Evaluation et de Traitement de la maladie de Gaucher (CETG)
Source: Journal of inherited metabolic disease [J Inherit Metab Dis] 2025 Mar; Vol. 48 (2), pp. e70026.
Publication Type: Journal Article
Journal Info: Publisher: Wiley Country of Publication: United States NLM ID: 7910918 Publication Model: Print Cited Medium: Internet ISSN: 1573-2665 (Electronic) Linking ISSN: 01418955 NLM ISO Abbreviation: J Inherit Metab Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1573-2665
DOI:10.1002/jimd.70026