Patients on treatment with risdiplam in Italy: challenges in the interpretation of the real-world data.
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| Title: | Patients on treatment with risdiplam in Italy: challenges in the interpretation of the real-world data. |
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| Authors: | Albamonte E; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Milan, Italy. emilio.albamonte@centrocliniconemo.it., Lizio A; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Milan, Italy., Coratti G; Pediatric Neuromuscular Unit, The NEMO Center in Rome, Rome, Italy.; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., Maggi L; Neuroimmunology and Neuromuscular Disease Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., Pegoraro E; Department of Neurosciences, University of Padova, Padua, Italy., Pane M; Pediatric Neurology, Department of Woman and Child Health and Public Health, Università Cattolica del Sacro Cuore, Child Health Area, Rome, Italy.; Pediatric Neuromuscular Unit, The NEMO Center in Rome, Rome, Italy., Messina S; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Masson R; Neuroimmunology and Neuromuscular Disease Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., D'Amico A; Unit of Muscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital, Rome, Italy., Bertini E; Unit of Muscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital, Rome, Italy., Pini A; Neuromuscular Pediatric Unit, UOC Di Neuropsichiatria Dell'età Pediatrica, IRCCS Istituto Delle Scienze Neurologiche Di Bologna, Bologna, Italy., Ricci F; Neuromuscular Center, AOU Città Della Salute E Della Scienza, University of Turin, Turin, Italy., Mongini T; Department of Neurosciences Rita Levi Montalcini, University of Turin, Turin, Italy., Bruno C; Centre of Translational and Experimental Myology, Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health-DINOGMI, IRCCS Istituto Giannina Gaslini, University of Genoa, Genoa, Italy., Patanella K; The NEMO Center in Rome, Adult Neuromuscular Unit, Rome, Italy., Sframeli M; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Dosi C; Neuroimmunology and Neuromuscular Disease Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., Bonanno S; Neuroimmunology and Neuromuscular Disease Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., Scarpini G; Neuromuscular Pediatric Unit, UOC Di Neuropsichiatria Dell'età Pediatrica, IRCCS Istituto Delle Scienze Neurologiche Di Bologna, Bologna, Italy., Brolatti N; Centre of Translational and Experimental Myology, Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health-DINOGMI, IRCCS Istituto Giannina Gaslini, University of Genoa, Genoa, Italy., Zanolini A; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Milan, Italy., Bravetti C; Pediatric Neuromuscular Unit, The NEMO Center in Rome, Rome, Italy., Pera MC; Pediatric Neuromuscular Unit, The NEMO Center in Rome, Rome, Italy., Mercuri EM; Pediatric Neuromuscular Unit, The NEMO Center in Rome, Rome, Italy. emilio.albamonte@centrocliniconemo.it.; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy. emilio.albamonte@centrocliniconemo.it., Sansone VA; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Milan, Italy. emilio.albamonte@centrocliniconemo.it. |
| Corporate Authors: | ItaSMAc |
| Source: | Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology [Neurol Sci] 2025 Aug; Vol. 46 (8), pp. 3839-3849. Date of Electronic Publication: 2025 Mar 28. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Springer-Verlag Italia Country of Publication: Italy NLM ID: 100959175 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1590-3478 (Electronic) Linking ISSN: 15901874 NLM ISO Abbreviation: Neurol Sci Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1590-3478 |
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| DOI: | 10.1007/s10072-025-08125-7 |
