Opinion of the Italian Association of Myology on Ataluren for the Treatment of Nonsense Mutation Duchenne Muscular Dystrophy.
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| Title: | Opinion of the Italian Association of Myology on Ataluren for the Treatment of Nonsense Mutation Duchenne Muscular Dystrophy. |
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| Authors: | Bello L; Department of Neurosciences, DNS Clinica Neurologica, Azienda Ospedale University of Padova, via Giustiniani, 5, 35121, Padua, Italy. luca.bello@unipd.it., Riguzzi P; Department of Neurosciences, DNS Clinica Neurologica, Azienda Ospedale University of Padova, via Giustiniani, 5, 35121, Padua, Italy., Albamonte E; The NeMO Center in Milan, Neurorehabilitation Unit, ASST Niguarda Hospital, University of Milan, Milan, Italy., Astrea G; Department of Neuroscience, IRCCS Stella Maris Foundation, Pisa, Italy., Battini R; Department of Neuroscience, IRCCS Stella Maris Foundation, Pisa, Italy.; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy., Barp A; Azienda Provinciale Servizi Sanitari (APSS) Trento, Trento, Italy., Berardinelli AL; C. Mondino Foundation, Pavia, Italy., Bertini ES; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy., Brolatti N; IRCCS Istituto Giannina Gaslini, Genoa, Italy., Bruno C; IRCCS Istituto Giannina Gaslini, Genoa, Italy.; Department of Neurosciences, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health (DINOGMI), University of Genova, Genoa, Italy., Corti S; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.; Department of Pathophysiology and Transplantation (DEPT), Dino Ferrari Centre, University of Milan, Milan, Italy., D'Amico A; Department of Pathophysiology and Transplantation (DEPT), Dino Ferrari Centre, University of Milan, Milan, Italy., D'Angelo MG; Scientific Institute IRCCS Eugenio Medea, Bosisio Parini, Italy., Dallavalle G; Azienda Sanitaria Locale 4 Chiavarese, Chiavari, Italy., Liguori R; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy., Maggi L; Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., Magri F; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy., Mancuso M; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., Masson R; Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., Mercuri E; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.; Università Cattolica del Sacro Cuore, Rome, Italy., Minetti C; IRCCS Istituto Giannina Gaslini, Genoa, Italy.; Department of Neurosciences, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health (DINOGMI), University of Genova, Genoa, Italy., Messina S; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Mongini T; Neuromuscular Unit, Department of Neurosciences RLM, University of Turin, Turin, Italy., Musumeci O; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Nigro V; Medical Genetics and Cardiomyology, University of Campania 'Luigi Vanvitelli', Naples, Italy., Pane M; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.; Università Cattolica del Sacro Cuore, Rome, Italy., Panicucci C; IRCCS Istituto Giannina Gaslini, Genoa, Italy., Pedemonte M; IRCCS Istituto Giannina Gaslini, Genoa, Italy., Pini A; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy., Politano L; Medical Genetics and Cardiomyology, University of Campania 'Luigi Vanvitelli', Naples, Italy., Previtali S; Neuromuscular Repair Unit, Institute of Experimental Neurology (InSpe), Division of Neuroscience, IRCCS Ospedale San Raffaele and Vita-Salute San Raffaele University, Milan, Italy., Ricci F; Neuromuscular Unit, Department of Neurosciences RLM, University of Turin, Turin, Italy., Ricci G; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy., Ruggiero L; Department of Neurosciences, Reproductive and Odontostomatological Sciences, University of Naples 'Federico II', Naples, Italy., Sansone V; The NeMO Center in Milan, Neurorehabilitation Unit, ASST Niguarda Hospital, University of Milan, Milan, Italy., Siciliano G; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy., Trabacca A; Scientific Institute IRCCS Eugenio Medea, Bosisio Parini, Italy., Trucco F; Department of Neurosciences, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health (DINOGMI), University of Genova, Genoa, Italy., Velardo D; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.; Department of Pathophysiology and Transplantation (DEPT), Dino Ferrari Centre, University of Milan, Milan, Italy., Pegoraro E; Department of Neurosciences, DNS Clinica Neurologica, Azienda Ospedale University of Padova, via Giustiniani, 5, 35121, Padua, Italy., Comi GP; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.; Department of Pathophysiology and Transplantation (DEPT), Dino Ferrari Centre, University of Milan, Milan, Italy. |
| Source: | Drugs in R&D [Drugs R D] 2025 Jun; Vol. 25 (2), pp. 99-106. Date of Electronic Publication: 2025 May 28. |
| Publication Type: | Journal Article; Review |
| Journal Info: | Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 100883647 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-6901 (Electronic) Linking ISSN: 11745886 NLM ISO Abbreviation: Drugs R D Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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