In utero lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells.
Saved in:
| Title: | In utero lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells. |
|---|---|
| Authors: | Worthington AK; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA., Borges B; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA., Lum T; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA., Echeverri ES; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology and Emory University School of Medicine, Atlanta, GA, 30332, USA., Zada FM; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA., Cordero MA; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA., Kim H; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology and Emory University School of Medicine, Atlanta, GA, 30332, USA., Zenhausern R; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology and Emory University School of Medicine, Atlanta, GA, 30332, USA., Celik O; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology and Emory University School of Medicine, Atlanta, GA, 30332, USA., Shaw C; Intellia Therapeutics, Cambridge, MA., Gutierrez-Martinez P; Intellia Therapeutics, Cambridge, MA., Omarova M; Intellia Therapeutics, Cambridge, MA., Blanchard C; Intellia Therapeutics, Cambridge, MA., Burns S; Intellia Therapeutics, Cambridge, MA., Cromer MK; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA., Dahlman JE; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology and Emory University School of Medicine, Atlanta, GA, 30332, USA., MacKenzie TC; Department of Surgery, University of California, San Francisco, CA, USA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, CA, USA.; The Center for Maternal-Fetal Precision Medicine, University of California, San Francisco, CA, USA. |
| Source: | BioRxiv : the preprint server for biology [bioRxiv] 2025 May 12. Date of Electronic Publication: 2025 May 12. |
| Publication Type: | Journal Article; Preprint |
| Journal Info: | Country of Publication: United States NLM ID: 101680187 Publication Model: Electronic Cited Medium: Internet ISSN: 2692-8205 (Electronic) Linking ISSN: 26928205 NLM ISO Abbreviation: bioRxiv Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
Be the first to leave a comment!