Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy.
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| Title: | Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy. |
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| Authors: | Valentini I; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy. ilaria.valentini@unicatt.it.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy. ilaria.valentini@unicatt.it., Ghetti G; AdRes HEOR s.r.l, Turin, Italy., Pane M; Pediatric Neurology Unit, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy.; Nemo Clinical Centre, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy., Rumi F; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy., Di Brino E; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy., Basile M; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy., Pistillo GM; Novartis Pharma AG, Basel, Switzerland., Bischof M; Novartis Pharma AG, Basel, Switzerland. |
| Source: | The European journal of health economics : HEPAC : health economics in prevention and care [Eur J Health Econ] 2026 Feb; Vol. 27 (1), pp. 77-94. Date of Electronic Publication: 2025 Jun 26. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Springer-Verlag Country of Publication: Germany NLM ID: 101134867 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1618-7601 (Electronic) Linking ISSN: 16187598 NLM ISO Abbreviation: Eur J Health Econ Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 40569556 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Valentini+I%22">Valentini I</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy. ilaria.valentini@unicatt.it.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy. ilaria.valentini@unicatt.it.<br /><searchLink fieldCode="AU" term="%22Ghetti+G%22">Ghetti G</searchLink>; AdRes HEOR s.r.l, Turin, Italy.<br /><searchLink fieldCode="AU" term="%22Pane+M%22">Pane M</searchLink>; Pediatric Neurology Unit, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy.; Nemo Clinical Centre, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Rumi+F%22">Rumi F</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Di+Brino+E%22">Di Brino E</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Basile+M%22">Basile M</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Pistillo+GM%22">Pistillo GM</searchLink>; Novartis Pharma AG, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Bischof+M%22">Bischof M</searchLink>; Novartis Pharma AG, Basel, Switzerland. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101134867%22">The European journal of health economics : HEPAC : health economics in prevention and care</searchLink> [Eur J Health Econ] 2026 Feb; Vol. 27 (1), pp. 77-94. <i>Date of Electronic Publication: </i>2025 Jun 26. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Springer-Verlag%22">Springer-Verlag </searchLink><i>Country of Publication: </i>Germany <i>NLM ID: </i>101134867 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1618-7601 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2216187598%22">16187598 </searchLink><i>NLM ISO Abbreviation: </i>Eur J Health Econ <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=40569556 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1007/s10198-025-01806-2 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 77 Titles: – TitleFull: Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Valentini I – PersonEntity: Name: NameFull: Ghetti G – PersonEntity: Name: NameFull: Pane M – PersonEntity: Name: NameFull: Rumi F – PersonEntity: Name: NameFull: Di Brino E – PersonEntity: Name: NameFull: Basile M – PersonEntity: Name: NameFull: Pistillo GM – PersonEntity: Name: NameFull: Bischof M IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 02 Text: 2026 Feb Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1618-7601 Numbering: – Type: volume Value: 27 – Type: issue Value: 1 Titles: – TitleFull: The European journal of health economics : HEPAC : health economics in prevention and care Type: main |
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