Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy.

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Title: Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy.
Authors: Valentini I; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy. ilaria.valentini@unicatt.it.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy. ilaria.valentini@unicatt.it., Ghetti G; AdRes HEOR s.r.l, Turin, Italy., Pane M; Pediatric Neurology Unit, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy.; Nemo Clinical Centre, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy., Rumi F; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy., Di Brino E; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy., Basile M; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy., Pistillo GM; Novartis Pharma AG, Basel, Switzerland., Bischof M; Novartis Pharma AG, Basel, Switzerland.
Source: The European journal of health economics : HEPAC : health economics in prevention and care [Eur J Health Econ] 2026 Feb; Vol. 27 (1), pp. 77-94. Date of Electronic Publication: 2025 Jun 26.
Publication Type: Journal Article
Journal Info: Publisher: Springer-Verlag Country of Publication: Germany NLM ID: 101134867 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1618-7601 (Electronic) Linking ISSN: 16187598 NLM ISO Abbreviation: Eur J Health Econ Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy.
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  Data: <searchLink fieldCode="AU" term="%22Valentini+I%22">Valentini I</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy. ilaria.valentini@unicatt.it.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy. ilaria.valentini@unicatt.it.<br /><searchLink fieldCode="AU" term="%22Ghetti+G%22">Ghetti G</searchLink>; AdRes HEOR s.r.l, Turin, Italy.<br /><searchLink fieldCode="AU" term="%22Pane+M%22">Pane M</searchLink>; Pediatric Neurology Unit, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy.; Nemo Clinical Centre, Fondazione Policlinico Universitario 'A. Gemelli,' IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Rumi+F%22">Rumi F</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Di+Brino+E%22">Di Brino E</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Basile+M%22">Basile M</searchLink>; Faculty of Economics, Cattolica del Sacro Cuore University (UCSC), Largo F, Vito 1, 00168, Rome, Italy.; Altems Advisory, Spin-off dell'Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Pistillo+GM%22">Pistillo GM</searchLink>; Novartis Pharma AG, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Bischof+M%22">Bischof M</searchLink>; Novartis Pharma AG, Basel, Switzerland.
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  Data: <searchLink fieldCode="JN" term="%22101134867%22">The European journal of health economics : HEPAC : health economics in prevention and care</searchLink> [Eur J Health Econ] 2026 Feb; Vol. 27 (1), pp. 77-94. <i>Date of Electronic Publication: </i>2025 Jun 26.
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        Value: 10.1007/s10198-025-01806-2
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        Text: English
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              Text: 2026 Feb
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              Y: 2026
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