Cost-effectiveness of treatments for presymptomatic newborn patients with spinal muscular atrophy and two or three copies of the survival motor neuron 2 gene in Italy. - Valentini I; Ghetti G; Pane M; Rumi F; Di Brino E; Basile M; Pistillo GM; Bischof M (The European journal of health economics : HEPAC : health economics in prevention and care, 2026)