View in EDS

Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2.

Saved in:
Bibliographic Details
Title: Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2.
Authors: Gibson RA; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, NC 27705, USA.; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Jeck WR; Department of Pathology, Duke University Medical Center, Durham, NC 27705, USA., Koch RL; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Jumani N; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Choi SJ; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Bali D; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Young SP; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Asokan A; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, NC 27705, USA.; Department of Surgery, Duke University Medical Center, Durham, NC 27705, USA., Lim JA; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA., Kishnani PS; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, NC 27705, USA.; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.
Source: Science advances [Sci Adv] 2025 Nov 14; Vol. 11 (46), pp. eady6760. Date of Electronic Publication: 2025 Nov 12.
Publication Type: Journal Article
Journal Info: Publisher: American Association for the Advancement of Science Country of Publication: United States NLM ID: 101653440 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2375-2548 (Electronic) Linking ISSN: 23752548 NLM ISO Abbreviation: Sci Adv Subsets: MEDLINE
Database: MEDLINE Ultimate
FullText Text:
  Availability: 0
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 41223291
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Gibson+RA%22">Gibson RA</searchLink>; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, NC 27705, USA.; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Jeck+WR%22">Jeck WR</searchLink>; Department of Pathology, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Koch+RL%22">Koch RL</searchLink>; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Jumani+N%22">Jumani N</searchLink>; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Choi+SJ%22">Choi SJ</searchLink>; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Bali+D%22">Bali D</searchLink>; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Young+SP%22">Young SP</searchLink>; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Asokan+A%22">Asokan A</searchLink>; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, NC 27705, USA.; Department of Surgery, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Lim+JA%22">Lim JA</searchLink>; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.<br /><searchLink fieldCode="AU" term="%22Kishnani+PS%22">Kishnani PS</searchLink>; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, NC 27705, USA.; Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27705, USA.
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22101653440%22">Science advances</searchLink> [Sci Adv] 2025 Nov 14; Vol. 11 (46), pp. eady6760. <i>Date of Electronic Publication: </i>2025 Nov 12.
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Journal Article
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Association+for+the+Advancement+of+Science%22">American Association for the Advancement of Science </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101653440 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2375-2548 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2223752548%22">23752548 </searchLink><i>NLM ISO Abbreviation: </i>Sci Adv <i>Subsets: </i>MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41223291
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1126/sciadv.ady6760
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        StartPage: eady6760
    Titles:
      – TitleFull: Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Gibson RA
      – PersonEntity:
          Name:
            NameFull: Jeck WR
      – PersonEntity:
          Name:
            NameFull: Koch RL
      – PersonEntity:
          Name:
            NameFull: Jumani N
      – PersonEntity:
          Name:
            NameFull: Choi SJ
      – PersonEntity:
          Name:
            NameFull: Bali D
      – PersonEntity:
          Name:
            NameFull: Young SP
      – PersonEntity:
          Name:
            NameFull: Asokan A
      – PersonEntity:
          Name:
            NameFull: Lim JA
      – PersonEntity:
          Name:
            NameFull: Kishnani PS
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 14
              M: 11
              Text: 2025 Nov 14
              Type: published
              Y: 2025
          Identifiers:
            – Type: issn-electronic
              Value: 2375-2548
          Numbering:
            – Type: volume
              Value: 11
            – Type: issue
              Value: 46
          Titles:
            – TitleFull: Science advances
              Type: main
ResultId 1