Charting the translational pathway: ISSCR best practices for the development of PSC-derived therapies.

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Title: Charting the translational pathway: ISSCR best practices for the development of PSC-derived therapies.
Authors: Barry J; Cell and Gene Therapy Catapult, Edinburgh and London, UK. Electronic address: jacqueline.barry@ct.catapult.org.uk., Abranches E; ViSync Technologies, Oeiras, Portugal., Baptista RP; SmartCella, Stockholm, Sweden., Barry C; Evanston, IL ISSCR, USA., Brandsten C; Takara Bio Europe, Gothenburg, Sweden., Bruce K; RoslinCT, Edinburgh, UK., Carpenter MK; Carpenter Consulting Corporation, Seattle, WA, USA., Cavagnaro J; Access Bio, Boyce, VA, USA., Collins L; California Institute for Regenerative Medicine, South San Francisco, CA, USA., Csaszar E; University Health Network, Toronto, ON, Canada., Dashnau J; Century Therapeutics, Philadelphia, PA, USA., de Villa D; Evanston, IL ISSCR, USA., Fynes K; eXmoor Pharma, Patchway, UK., Gabaldo M; Aptuit (Verona) srl, an Evotec company, Verona, Italy., Hao J; National Stem Cell Resource Center, Beijing, China., Harel-Adar T; MatriCelf, Ness Ziona, Israel., Hei D; Kenai Therapeutics, San Diego, CA, USA., Henchcliffe C; University of California, Irvine, Irvine, CA, USA., Hidalgo-Simon A; Leiden University Medical Center & reNEW, The Netherlands., Hollands J; Cell Therapies Pty Ltd, Melbourne, VIC, Australia., Hursh D; Hursh Cell Therapy Consulting, LLC, Silver Spring, MD, USA., Jackman S; Charles River Laboratories, Shrewsbury, MA, USA., Kelly K; Cynata Therapeutics Limited, Melbourne, VIC, Australia., Kim JH; Ajou University, Seoul, Korea., Kim H; Korean National Institute of Health, Cheongju, Korea., Kino-Oka M; The University of Osaka, Osaka, Japan., Lakshmipathy U; Thermo Fisher Scientific, San Diego, CA, USA., Lamb T; Evanston, IL ISSCR, USA., Lazic SE; Prioris.ai Inc., Ottawa, ON, Canada., Loring JF; Scripps Research and Aspen Neuroscience, San Diego, CA, USA., Ludwig TE; WiCell Research Institute, Madison, WI, USA., Mariappan I; Institute for Stem Cell Science and Regenerative Medicine, Bengaluru, India., Monville C; Université Paris-Saclay, University Evry, INSERM, I-Stem, Corbeil-Essonnes, France., Mountford JC; Scottish National Blood Transfusion Service, Edinburgh, UK., Nagy A; Lunenfeld-Tanenbaum Research Institute, Sinai Health, Toronto, ON, Canada., Okano H; Keio University Regenerative Medicine Research Center, Kawasaki, Kanagawa, Japan., Pellegrini G; University of Modena and Reggio Emilia, Modena, Italy., Persson A; AstraZeneca, Gothenburg, Sweden., Prutton K; Evanston, IL ISSCR, USA., Rasko JEJ; Sydney, NSW, Australia., Sareen D; Biomanufacturing Center, Cedars-Sinai Medical Center, Los Angeles, CA, USA., Sato Y; National Institute of Health Sciences, Kawasaki, Kanagawa, Japan., Shnaiderman A; MatriCelf, Ness Ziona, Israel., Stacey G; International Cell Banking Initiative, Barley, UK., Svendsen CN; Cedars-Sinai Board of Governors Regenerative Medicine Institute, Los Angeles, CA, USA., Tomishima M; BlueRock Therapeutics, New York, NY, USA., Trounson A; Catherics and Monash University, Melbourne, VIC, Australia., Viswanathan S; University Health Network, Toronto, ON, Canada., Wang S; Zephrym, Beijing, China., Wydenbach K; Weatherden, London, UK., Zhang A; Zephrym, Beijing, China., Zylberberg C; Akron Bio, Boca Raton, FL, USA., Mosher JT; Evanston, IL ISSCR, USA. Electronic address: jmosher@isscr.org., Bharti K; National Institutes of Health, Bethesda, MD, USA. Electronic address: kapil.bharti@nih.gov.
Source: Stem cell reports [Stem Cell Reports] 2026 Feb 10; Vol. 21 (2), pp. 102784. Date of Electronic Publication: 2026 Jan 22.
Publication Type: Journal Article; Review
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101611300 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2213-6711 (Electronic) Linking ISSN: 22136711 NLM ISO Abbreviation: Stem Cell Reports Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Barry+J%22">Barry J</searchLink>; Cell and Gene Therapy Catapult, Edinburgh and London, UK. Electronic address: jacqueline.barry@ct.catapult.org.uk.<br /><searchLink fieldCode="AU" term="%22Abranches+E%22">Abranches E</searchLink>; ViSync Technologies, Oeiras, Portugal.<br /><searchLink fieldCode="AU" term="%22Baptista+RP%22">Baptista RP</searchLink>; SmartCella, Stockholm, Sweden.<br /><searchLink fieldCode="AU" term="%22Barry+C%22">Barry C</searchLink>; Evanston, IL ISSCR, USA.<br /><searchLink fieldCode="AU" term="%22Brandsten+C%22">Brandsten C</searchLink>; Takara Bio Europe, Gothenburg, Sweden.<br /><searchLink fieldCode="AU" term="%22Bruce+K%22">Bruce K</searchLink>; RoslinCT, Edinburgh, UK.<br /><searchLink fieldCode="AU" term="%22Carpenter+MK%22">Carpenter MK</searchLink>; Carpenter Consulting Corporation, Seattle, WA, USA.<br /><searchLink fieldCode="AU" term="%22Cavagnaro+J%22">Cavagnaro J</searchLink>; Access Bio, Boyce, VA, USA.<br /><searchLink fieldCode="AU" term="%22Collins+L%22">Collins L</searchLink>; California Institute for Regenerative Medicine, South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Csaszar+E%22">Csaszar E</searchLink>; University Health Network, Toronto, ON, Canada.<br /><searchLink fieldCode="AU" term="%22Dashnau+J%22">Dashnau J</searchLink>; Century Therapeutics, Philadelphia, PA, USA.<br /><searchLink fieldCode="AU" term="%22de+Villa+D%22">de Villa D</searchLink>; Evanston, IL ISSCR, USA.<br /><searchLink fieldCode="AU" term="%22Fynes+K%22">Fynes K</searchLink>; eXmoor Pharma, Patchway, UK.<br /><searchLink fieldCode="AU" term="%22Gabaldo+M%22">Gabaldo M</searchLink>; Aptuit (Verona) srl, an Evotec company, Verona, Italy.<br /><searchLink fieldCode="AU" term="%22Hao+J%22">Hao J</searchLink>; National Stem Cell Resource Center, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Harel-Adar+T%22">Harel-Adar T</searchLink>; MatriCelf, Ness Ziona, Israel.<br /><searchLink fieldCode="AU" term="%22Hei+D%22">Hei D</searchLink>; Kenai Therapeutics, San Diego, CA, USA.<br /><searchLink fieldCode="AU" term="%22Henchcliffe+C%22">Henchcliffe C</searchLink>; University of California, Irvine, Irvine, CA, USA.<br /><searchLink fieldCode="AU" term="%22Hidalgo-Simon+A%22">Hidalgo-Simon A</searchLink>; Leiden University Medical Center & reNEW, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Hollands+J%22">Hollands J</searchLink>; Cell Therapies Pty Ltd, Melbourne, VIC, Australia.<br /><searchLink fieldCode="AU" term="%22Hursh+D%22">Hursh D</searchLink>; Hursh Cell Therapy Consulting, LLC, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Jackman+S%22">Jackman S</searchLink>; Charles River Laboratories, Shrewsbury, MA, USA.<br /><searchLink fieldCode="AU" term="%22Kelly+K%22">Kelly K</searchLink>; Cynata Therapeutics Limited, Melbourne, VIC, Australia.<br /><searchLink fieldCode="AU" term="%22Kim+JH%22">Kim JH</searchLink>; Ajou University, Seoul, Korea.<br /><searchLink fieldCode="AU" term="%22Kim+H%22">Kim H</searchLink>; Korean National Institute of Health, Cheongju, Korea.<br /><searchLink fieldCode="AU" term="%22Kino-Oka+M%22">Kino-Oka M</searchLink>; The University of Osaka, Osaka, Japan.<br /><searchLink fieldCode="AU" term="%22Lakshmipathy+U%22">Lakshmipathy U</searchLink>; Thermo Fisher Scientific, San Diego, CA, USA.<br /><searchLink fieldCode="AU" term="%22Lamb+T%22">Lamb T</searchLink>; Evanston, IL ISSCR, USA.<br /><searchLink fieldCode="AU" term="%22Lazic+SE%22">Lazic SE</searchLink>; Prioris.ai Inc., Ottawa, ON, Canada.<br /><searchLink fieldCode="AU" term="%22Loring+JF%22">Loring JF</searchLink>; Scripps Research and Aspen Neuroscience, San Diego, CA, USA.<br /><searchLink fieldCode="AU" term="%22Ludwig+TE%22">Ludwig TE</searchLink>; WiCell Research Institute, Madison, WI, USA.<br /><searchLink fieldCode="AU" term="%22Mariappan+I%22">Mariappan I</searchLink>; Institute for Stem Cell Science and Regenerative Medicine, Bengaluru, India.<br /><searchLink fieldCode="AU" term="%22Monville+C%22">Monville C</searchLink>; Université Paris-Saclay, University Evry, INSERM, I-Stem, Corbeil-Essonnes, France.<br /><searchLink fieldCode="AU" term="%22Mountford+JC%22">Mountford JC</searchLink>; Scottish National Blood Transfusion Service, Edinburgh, UK.<br /><searchLink fieldCode="AU" term="%22Nagy+A%22">Nagy A</searchLink>; Lunenfeld-Tanenbaum Research Institute, Sinai Health, Toronto, ON, Canada.<br /><searchLink fieldCode="AU" term="%22Okano+H%22">Okano H</searchLink>; Keio University Regenerative Medicine Research Center, Kawasaki, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Pellegrini+G%22">Pellegrini G</searchLink>; University of Modena and Reggio Emilia, Modena, Italy.<br /><searchLink fieldCode="AU" term="%22Persson+A%22">Persson A</searchLink>; AstraZeneca, Gothenburg, Sweden.<br /><searchLink fieldCode="AU" term="%22Prutton+K%22">Prutton K</searchLink>; Evanston, IL ISSCR, USA.<br /><searchLink fieldCode="AU" term="%22Rasko+JEJ%22">Rasko JEJ</searchLink>; Sydney, NSW, Australia.<br /><searchLink fieldCode="AU" term="%22Sareen+D%22">Sareen D</searchLink>; Biomanufacturing Center, Cedars-Sinai Medical Center, Los Angeles, CA, USA.<br /><searchLink fieldCode="AU" term="%22Sato+Y%22">Sato Y</searchLink>; National Institute of Health Sciences, Kawasaki, Kanagawa, Japan.<br /><searchLink fieldCode="AU" term="%22Shnaiderman+A%22">Shnaiderman A</searchLink>; MatriCelf, Ness Ziona, Israel.<br /><searchLink fieldCode="AU" term="%22Stacey+G%22">Stacey G</searchLink>; International Cell Banking Initiative, Barley, UK.<br /><searchLink fieldCode="AU" term="%22Svendsen+CN%22">Svendsen CN</searchLink>; Cedars-Sinai Board of Governors Regenerative Medicine Institute, Los Angeles, CA, USA.<br /><searchLink fieldCode="AU" term="%22Tomishima+M%22">Tomishima M</searchLink>; BlueRock Therapeutics, New York, NY, USA.<br /><searchLink fieldCode="AU" term="%22Trounson+A%22">Trounson A</searchLink>; Catherics and Monash University, Melbourne, VIC, Australia.<br /><searchLink fieldCode="AU" term="%22Viswanathan+S%22">Viswanathan S</searchLink>; University Health Network, Toronto, ON, Canada.<br /><searchLink fieldCode="AU" term="%22Wang+S%22">Wang S</searchLink>; Zephrym, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Wydenbach+K%22">Wydenbach K</searchLink>; Weatherden, London, UK.<br /><searchLink fieldCode="AU" term="%22Zhang+A%22">Zhang A</searchLink>; Zephrym, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Zylberberg+C%22">Zylberberg C</searchLink>; Akron Bio, Boca Raton, FL, USA.<br /><searchLink fieldCode="AU" term="%22Mosher+JT%22">Mosher JT</searchLink>; Evanston, IL ISSCR, USA. Electronic address: jmosher@isscr.org.<br /><searchLink fieldCode="AU" term="%22Bharti+K%22">Bharti K</searchLink>; National Institutes of Health, Bethesda, MD, USA. Electronic address: kapil.bharti@nih.gov.
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