Divalent siRNA for prion disease.
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| Title: | Divalent siRNA for prion disease. |
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| Authors: | Gentile JE; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Corridon TL; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Serack FE; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Echeverria D; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Kennedy ZC; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Gallant-Behm CL; Atalanta Therapeutics, Boston, MA 02210, United States., Hassler MR; Atalanta Therapeutics, Boston, MA 02210, United States., Kinberger GA; Atalanta Therapeutics, Boston, MA 02210, United States., Kelemen MN; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Kamath NG; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Lian Y; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Gross KY; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Miller R; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., DeSouza-Lenz K; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Howard M; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Guzman K; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Chan N; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Laversenne V; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Curtis D; Atalanta Therapeutics, Boston, MA 02210, United States., Fettes K; FTS Pharma Consulting LLC, Medfield, MA 02052, United States., Lemaitre M; ML Consult LLC, Cincinnati, OH 45220, United States., Jackson AL; Atalanta Therapeutics, Boston, MA 02210, United States., Yamada K; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Alterman JF; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Coffey AA; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Minikel EV; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.; McCance Center for Brain Health and Department of Neurology, Massachusetts General Hospital, Boston, MA 02114, United States.; Department of Neurology, Harvard Medical School, Boston, MA 02115, United States.; Prion Alliance, Cambridge, MA 02139, United States., Khvorova A; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Vallabh SM; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.; McCance Center for Brain Health and Department of Neurology, Massachusetts General Hospital, Boston, MA 02114, United States.; Department of Neurology, Harvard Medical School, Boston, MA 02115, United States.; Prion Alliance, Cambridge, MA 02139, United States. |
| Source: | Nucleic acids research [Nucleic Acids Res] 2026 Apr 23; Vol. 54 (8). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN: 1362-4962 (Electronic) Linking ISSN: 03051048 NLM ISO Abbreviation: Nucleic Acids Res Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 42033217 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Divalent siRNA for prion disease. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Gentile+JE%22">Gentile JE</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Corridon+TL%22">Corridon TL</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Serack+FE%22">Serack FE</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Echeverria+D%22">Echeverria D</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22Kennedy+ZC%22">Kennedy ZC</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22Gallant-Behm+CL%22">Gallant-Behm CL</searchLink>; Atalanta Therapeutics, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Hassler+MR%22">Hassler MR</searchLink>; Atalanta Therapeutics, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Kinberger+GA%22">Kinberger GA</searchLink>; Atalanta Therapeutics, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Kelemen+MN%22">Kelemen MN</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Kamath+NG%22">Kamath NG</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Lian+Y%22">Lian Y</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Gross+KY%22">Gross KY</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22Miller+R%22">Miller R</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22DeSouza-Lenz+K%22">DeSouza-Lenz K</searchLink>; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Howard+M%22">Howard M</searchLink>; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Guzman+K%22">Guzman K</searchLink>; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Chan+N%22">Chan N</searchLink>; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Laversenne+V%22">Laversenne V</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Curtis+D%22">Curtis D</searchLink>; Atalanta Therapeutics, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Fettes+K%22">Fettes K</searchLink>; FTS Pharma Consulting LLC, Medfield, MA 02052, United States.<br /><searchLink fieldCode="AU" term="%22Lemaitre+M%22">Lemaitre M</searchLink>; ML Consult LLC, Cincinnati, OH 45220, United States.<br /><searchLink fieldCode="AU" term="%22Jackson+AL%22">Jackson AL</searchLink>; Atalanta Therapeutics, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Yamada+K%22">Yamada K</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22Alterman+JF%22">Alterman JF</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22Coffey+AA%22">Coffey AA</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.<br /><searchLink fieldCode="AU" term="%22Minikel+EV%22">Minikel EV</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.; McCance Center for Brain Health and Department of Neurology, Massachusetts General Hospital, Boston, MA 02114, United States.; Department of Neurology, Harvard Medical School, Boston, MA 02115, United States.; Prion Alliance, Cambridge, MA 02139, United States.<br /><searchLink fieldCode="AU" term="%22Khvorova+A%22">Khvorova A</searchLink>; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States.<br /><searchLink fieldCode="AU" term="%22Vallabh+SM%22">Vallabh SM</searchLink>; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.; McCance Center for Brain Health and Department of Neurology, Massachusetts General Hospital, Boston, MA 02114, United States.; Department of Neurology, Harvard Medical School, Boston, MA 02115, United States.; Prion Alliance, Cambridge, MA 02139, United States. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%220411011%22">Nucleic acids research</searchLink> [Nucleic Acids Res] 2026 Apr 23; Vol. 54 (8). – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Oxford+University+Press%22">Oxford University Press </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>0411011 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1362-4962 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203051048%22">03051048 </searchLink><i>NLM ISO Abbreviation: </i>Nucleic Acids Res <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42033217 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1093/nar/gkag287 Languages: – Code: eng Text: English Titles: – TitleFull: Divalent siRNA for prion disease. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Gentile JE – PersonEntity: Name: NameFull: Corridon TL – PersonEntity: Name: NameFull: Serack FE – PersonEntity: Name: NameFull: Echeverria D – PersonEntity: Name: NameFull: Kennedy ZC – PersonEntity: Name: NameFull: Gallant-Behm CL – PersonEntity: Name: NameFull: Hassler MR – PersonEntity: Name: NameFull: Kinberger GA – PersonEntity: Name: NameFull: Kelemen MN – PersonEntity: Name: NameFull: Kamath NG – PersonEntity: Name: NameFull: Lian Y – PersonEntity: Name: NameFull: Gross KY – PersonEntity: Name: NameFull: Miller R – PersonEntity: Name: NameFull: DeSouza-Lenz K – PersonEntity: Name: NameFull: Howard M – PersonEntity: Name: NameFull: Guzman K – PersonEntity: Name: NameFull: Chan N – PersonEntity: Name: NameFull: Laversenne V – PersonEntity: Name: NameFull: Curtis D – PersonEntity: Name: NameFull: Fettes K – PersonEntity: Name: NameFull: Lemaitre M – PersonEntity: Name: NameFull: Jackson AL – PersonEntity: Name: NameFull: Yamada K – PersonEntity: Name: NameFull: Alterman JF – PersonEntity: Name: NameFull: Coffey AA – PersonEntity: Name: NameFull: Minikel EV – PersonEntity: Name: NameFull: Khvorova A – PersonEntity: Name: NameFull: Vallabh SM IsPartOfRelationships: – BibEntity: Dates: – D: 23 M: 04 Text: 2026 Apr 23 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1362-4962 Numbering: – Type: volume Value: 54 – Type: issue Value: 8 Titles: – TitleFull: Nucleic acids research Type: main |
| ResultId | 1 |