Divalent siRNA for prion disease.

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Title: Divalent siRNA for prion disease.
Authors: Gentile JE; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Corridon TL; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Serack FE; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Echeverria D; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Kennedy ZC; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Gallant-Behm CL; Atalanta Therapeutics, Boston, MA 02210, United States., Hassler MR; Atalanta Therapeutics, Boston, MA 02210, United States., Kinberger GA; Atalanta Therapeutics, Boston, MA 02210, United States., Kelemen MN; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Kamath NG; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Lian Y; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Gross KY; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Miller R; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., DeSouza-Lenz K; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Howard M; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Guzman K; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Chan N; Comparative Medicine, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Laversenne V; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Curtis D; Atalanta Therapeutics, Boston, MA 02210, United States., Fettes K; FTS Pharma Consulting LLC, Medfield, MA 02052, United States., Lemaitre M; ML Consult LLC, Cincinnati, OH 45220, United States., Jackson AL; Atalanta Therapeutics, Boston, MA 02210, United States., Yamada K; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Alterman JF; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Coffey AA; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States., Minikel EV; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.; McCance Center for Brain Health and Department of Neurology, Massachusetts General Hospital, Boston, MA 02114, United States.; Department of Neurology, Harvard Medical School, Boston, MA 02115, United States.; Prion Alliance, Cambridge, MA 02139, United States., Khvorova A; RNA Therapeutics Institute, UMass Chan Medical School, Worcester, MA 01605, United States., Vallabh SM; Program in Brain Health, Broad Institute of MIT and Harvard, Cambridge, MA 02142, United States.; McCance Center for Brain Health and Department of Neurology, Massachusetts General Hospital, Boston, MA 02114, United States.; Department of Neurology, Harvard Medical School, Boston, MA 02115, United States.; Prion Alliance, Cambridge, MA 02139, United States.
Source: Nucleic acids research [Nucleic Acids Res] 2026 Apr 23; Vol. 54 (8).
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN: 1362-4962 (Electronic) Linking ISSN: 03051048 NLM ISO Abbreviation: Nucleic Acids Res Subsets: MEDLINE
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