Base editing and nanoparticle transfection of airway cell types essential for treatment of cystic fibrosis.

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Title: Base editing and nanoparticle transfection of airway cell types essential for treatment of cystic fibrosis.
Authors: Kavanagh EW; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Department of Biomedical Engineering and., Joynt AT; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Pion AR; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Eastman AC; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Parr AI; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Starego KL; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Jain M; Department of Biomedical Engineering and., Shannon SR; Department of Biomedical Engineering and., Yoo EJ; Department of Biomedical Engineering and., Newby GA; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Institute for NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA., Tzeng SY; Department of Biomedical Engineering and., Sharma N; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Green JJ; Department of Biomedical Engineering and.; Institute for NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA., Cutting GR; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
Source: JCI insight [JCI Insight] 2026 May 08; Vol. 11 (9). Date of Electronic Publication: 2026 May 08 (Print Publication: 2026).
Publication Type: Journal Article
Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 101676073 Publication Model: eCollection Cited Medium: Internet ISSN: 2379-3708 (Electronic) Linking ISSN: 23793708 NLM ISO Abbreviation: JCI Insight Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Base editing and nanoparticle transfection of airway cell types essential for treatment of cystic fibrosis.
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  Data: <searchLink fieldCode="AU" term="%22Kavanagh+EW%22">Kavanagh EW</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Department of Biomedical Engineering and.<br /><searchLink fieldCode="AU" term="%22Joynt+AT%22">Joynt AT</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Pion+AR%22">Pion AR</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Eastman+AC%22">Eastman AC</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Parr+AI%22">Parr AI</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Starego+KL%22">Starego KL</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Jain+M%22">Jain M</searchLink>; Department of Biomedical Engineering and.<br /><searchLink fieldCode="AU" term="%22Shannon+SR%22">Shannon SR</searchLink>; Department of Biomedical Engineering and.<br /><searchLink fieldCode="AU" term="%22Yoo+EJ%22">Yoo EJ</searchLink>; Department of Biomedical Engineering and.<br /><searchLink fieldCode="AU" term="%22Newby+GA%22">Newby GA</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Institute for NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Tzeng+SY%22">Tzeng SY</searchLink>; Department of Biomedical Engineering and.<br /><searchLink fieldCode="AU" term="%22Sharma+N%22">Sharma N</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Green+JJ%22">Green JJ</searchLink>; Department of Biomedical Engineering and.; Institute for NanoBioTechnology, Johns Hopkins University, Baltimore, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Cutting+GR%22">Cutting GR</searchLink>; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
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  Data: <searchLink fieldCode="JN" term="%22101676073%22">JCI insight</searchLink> [JCI Insight] 2026 May 08; Vol. 11 (9). <i>Date of Electronic Publication: </i>2026 May 08 (<i>Print Publication: </i>2026).
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Society+for+Clinical+Investigation%22">American Society for Clinical Investigation </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101676073 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Internet <i>ISSN: </i>2379-3708 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2223793708%22">23793708 </searchLink><i>NLM ISO Abbreviation: </i>JCI Insight <i>Subsets: </i>MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42100873
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        Value: 10.1172/jci.insight.198563
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              Text: 2026 May 08
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