Preliminary insights into RNA in CSF of pediatric SMA patients after 6 months of nusinersen.

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Title: Preliminary insights into RNA in CSF of pediatric SMA patients after 6 months of nusinersen.
Authors: Garofalo, M.1 (AUTHOR), Bonanno, S.2 (AUTHOR), Marcuzzo, S.2 (AUTHOR), Pandini, C.3 (AUTHOR), Scarian, E.1 (AUTHOR), Dragoni, F.1,4 (AUTHOR), Di Gerlando, R.1,4 (AUTHOR), Bordoni, M.1 (AUTHOR), Parravicini, S.1,5 (AUTHOR), Gellera, C.6 (AUTHOR), Masson, R.2 (AUTHOR), Dosi, C.2 (AUTHOR), Zanin, R.2 (AUTHOR), Pansarasa, O.1 (AUTHOR) orietta.pansarasa@mondino.it, Cereda, C.7 (AUTHOR), Berardinelli, A.1 (AUTHOR), Gagliardi, S.1 (AUTHOR)
Source: Biology Direct. 9/13/2023, Vol. 18 Issue 1, p1-13. 13p.
Database: Academic Search Ultimate
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ISSN:17456150
DOI:10.1186/s13062-023-00413-6