Efficacy of tranilast in preventing exacerbating cardiac function and death from heart failure in muscular dystrophy patients with advanced-stage heart failure: a single-arm, open-label, multicenter study.

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Title: Efficacy of tranilast in preventing exacerbating cardiac function and death from heart failure in muscular dystrophy patients with advanced-stage heart failure: a single-arm, open-label, multicenter study.
Authors: Matsumura, Tsuyoshi1 (AUTHOR) matsumura.tsuyoshi.kq@mail.hosp.go.jp, Fukudome, Takayasu2 (AUTHOR), Motoyoshi, Yasufumi3 (AUTHOR), Nakamura, Akinori4 (AUTHOR), Kuru, Satoshi5 (AUTHOR), Segawa, Kazuhiko6 (AUTHOR), Kitao, Ruriko7 (AUTHOR), Watanabe, Chigusa8 (AUTHOR), Tamura, Takuhisa9 (AUTHOR), Takahashi, Toshiaki10 (AUTHOR), Hashimoto, Hiroya11 (AUTHOR), Sekimizu, Masahiro11 (AUTHOR), Saito, Akiko M.11 (AUTHOR), Asakura, Masanori12 (AUTHOR), Kimura, Koichi13 (AUTHOR), Iwata, Yuko14 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 1/9/2025, Vol. 20 Issue 1, p1-9. 9p.
Database: Academic Search Ultimate
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ISSN:17501172
DOI:10.1186/s13023-025-03538-1