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Analysis of the Italian cohort of late-onset Pompe disease (LOPD) patients after 10 and 15 years of therapy with alglucosidase alfa.

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Bibliographic Details
Title: Analysis of the Italian cohort of late-onset Pompe disease (LOPD) patients after 10 and 15 years of therapy with alglucosidase alfa.
Authors: Mongini, T.1 (AUTHOR) tizianaenrica.mongini@unito.it, Gadaleta, G.1 (AUTHOR), Alonge, P.2 (AUTHOR), Vercelli, L.1 (AUTHOR), Stura, I.3 (AUTHOR), Musumeci, O.4 (AUTHOR), Ravaglia, S.5 (AUTHOR), Ruggiero, L.6 (AUTHOR), Fiumara, A.7 (AUTHOR), Barone, R.7 (AUTHOR), Servidei, S.8,9 (AUTHOR), Sancricca, C.8,10 (AUTHOR), Siciliano, G.11 (AUTHOR), Ricci, G.11 (AUTHOR), Sechi, A.12 (AUTHOR), Tonin, P.13 (AUTHOR), Pegoraro, E.14 (AUTHOR), Filosto, M.15 (AUTHOR), D’Angelo, G.16 (AUTHOR), Comi, G.17 (AUTHOR)
Source: Journal of Neurology. Aug2025, Vol. 272 Issue 8, p1-12. 12p.
Database: Academic Search Ultimate
Description
ISSN:03405354
DOI:10.1007/s00415-025-13206-w