Treatment of dysferlinopathy with deflazacort: a double-blind, placebo-controlled clinical trial.

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Bibliographic Details
Title: Treatment of dysferlinopathy with deflazacort: a double-blind, placebo-controlled clinical trial.
Authors: Walter, Maggie C.1 maggie.walter@lrz.uni-muenchen.de, Reilich, Peter1, Thiele, Simone1, Schessl, Joachim1, Schreiber, Herbert2, Reiners, Karlheinz3, Kress, Wolfram4, Müller-Reible, Clemens4, Vorgerd, Matthias5, Urban, Peter6, Schrank, Bertold7, Deschauer, Marcus8, Schlotter-Weigel, Beate1, Kohnen, Ralf9, Lochmüller, Hanns10
Source: Orphanet Journal of Rare Diseases. 2013, Vol. 8 Issue 1, Special section p1-15. 15p. 1 Color Photograph, 1 Diagram, 5 Charts, 1 Graph.
Database: Academic Search Ultimate
Description
ISSN:17501172
DOI:10.1186/1750-1172-8-26