High dose sapropterin dihydrochloride therapy improves monoamine neurotransmitter turnover in murine phenylketonuria (PKU).

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Bibliographic Details
Title: High dose sapropterin dihydrochloride therapy improves monoamine neurotransmitter turnover in murine phenylketonuria (PKU).
Authors: Winn SR; Department of Molecular and Medical Genetics, Oregon Health & Science University, Mailstop L-103, 3181 Sam Jackson Park Rd., Portland, OR 97239, USA., Scherer T; Department of Pediatrics, University of Zurich, Steinweissstrasse 75, Zurich CH-8032, Switzerland., Thöny B; Department of Pediatrics, University of Zurich, Steinweissstrasse 75, Zurich CH-8032, Switzerland., Harding CO; Department of Molecular and Medical Genetics, Oregon Health & Science University, Mailstop L-103, 3181 Sam Jackson Park Rd., Portland, OR 97239, USA. Electronic address: hardingc@ohsu.edu.
Source: Molecular genetics and metabolism [Mol Genet Metab] 2016 Jan; Vol. 117 (1), pp. 5-11. Date of Electronic Publication: 2015 Nov 26.
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Academic Press Country of Publication: United States NLM ID: 9805456 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-7206 (Electronic) Linking ISSN: 10967192 NLM ISO Abbreviation: Mol Genet Metab Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1096-7206
DOI:10.1016/j.ymgme.2015.11.012