| Authors: |
Pastore N; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, 77030, USA. pastore@tigem.it.; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, 77030, USA. pastore@tigem.it., Huynh T; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, 77030, USA.; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, 77030, USA., Herz NJ; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, 77030, USA.; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, 77030, USA., Calcagni' A; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, 77030, USA.; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, 77030, USA., Klisch TJ; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, 77030, USA.; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, 77030, USA., Brunetti L; Stem Cells and Regenerative Medicine Center, Baylor College of Medicine, Houston, TX, 77030, USA.; Center for Cell and Gene Therapy, Baylor College of Medicine, Houston, TX, 77030, USA., Kim KH; Department of Molecular and Cell Biology, Baylor College of Medicine, Houston, TX, 77030, USA., De Giorgi M; Department of Molecular Physiology and Biophysics, Baylor College of Medicine, Houston, TX, 77030, USA., Hurley A; Department of Molecular Physiology and Biophysics, Baylor College of Medicine, Houston, TX, 77030, USA., Carissimo A; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, NA, 80078, Italy., Mutarelli M; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, NA, 80078, Italy., Aleksieva N; MRC Centre for Regenerative Medicine, University of Edinburgh, Edinburgh, EH16 4UU, UK., D'Orsi L; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, NA, 80078, Italy., Lagor WR; Department of Molecular Physiology and Biophysics, Baylor College of Medicine, Houston, TX, 77030, USA., Moore DD; Department of Molecular and Cell Biology, Baylor College of Medicine, Houston, TX, 77030, USA., Settembre C; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, NA, 80078, Italy.; Department of Translational Medicine, Medical Genetics, Federico II University, Naples, 80131, Italy., Finegold MJ; Department of Pathology, Baylor College of Medicine, Houston, TX, 77030, USA., Forbes SJ; MRC Centre for Regenerative Medicine, University of Edinburgh, Edinburgh, EH16 4UU, UK., Ballabio A; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, 77030, USA. ballabio@tigem.it.; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, 77030, USA. ballabio@tigem.it.; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, NA, 80078, Italy. ballabio@tigem.it.; Department of Translational Medicine, Medical Genetics, Federico II University, Naples, 80131, Italy. ballabio@tigem.it. |