| Authors: |
Savarirayan R; Murdoch Children's Research Institute, Royal Children's Hospital, and University of Melbourne, Parkville, VIC, Australia. Electronic address: ravi.savarirayan@vcgs.org.au., Tofts L; Kids Rehab, The Children's Hospital at Westmead, Westmead, NSW, Australia., Irving M; Guy's and St Thomas' NHS Foundation Trust, Evelina Children's Hospital, London, UK., Wilcox W; Emory University, Atlanta, Georgia, USA., Bacino CA; Baylor College of Medicine, Houston, TX, USA., Hoover-Fong J; McKusick-Nathans Department of Genetic Medicine, Johns Hopkins University, Baltimore, MD, USA., Ullot Font R; Hospital Sant Joan de Déu, Barcelona, Spain., Harmatz P; UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA., Rutsch F; Department of General Pediatrics, Muenster University Children's Hospital, Muenster, Germany., Bober MB; Nemours-Alfred I. du Pont Hospital for Children, Wilmington, DE, USA., Polgreen LE; Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA, USA., Ginebreda I; Hospital Universitario Quirón Dexeus, Barcelona, Spain., Mohnike K; Otto-von-Guericke-Universität, Magdeburg, Germany., Charrow J; Ann and Robert H Lurie Children's Hospital of Chicago, Chicago, IL, USA., Hoernschemeyer D; University of Missouri-Columbia, Columbia, MO, USA., Ozono K; Osaka University Hospital, Osaka, Japan., Alanay Y; Acibadem Mehmet Ali Aydiniar University, School of Medicine, Istanbul, Turkey., Arundel P; Sheffield Children's NHS Foundation Trust, Sheffield Children's Hospital, Sheffield, UK., Kagami S; Tokushima University Hospital, Tokushima, Japan., Yasui N; Tokushima University Hospital, Tokushima, Japan., White KK; Seattle Children's Hospital, Seattle, WA, USA., Saal HM; Cincinnati Children's Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, OH, USA., Leiva-Gea A; Hospital Universitario Virgen de la Victoria, Málaga, Spain., Luna-González F; Hospital Universitario Virgen de la Victoria, Málaga, Spain., Mochizuki H; Saitama Children's Hospital, Saitama, Japan., Basel D; Medical College of Wisconsin, Milwaukee, WI, USA., Porco DM; BioMarin Pharmaceutical, Novato, CA, USA., Jayaram K; BioMarin Pharmaceutical, Novato, CA, USA., Fisheleva E; BioMarin (UK), London, UK., Huntsman-Labed A; BioMarin (UK), London, UK., Day J; BioMarin (UK), London, UK. |