Sustained remission after haploidentical bone marrow transplantation in a child with refractory systemic juvenile idiopathic arthritis.

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Title: Sustained remission after haploidentical bone marrow transplantation in a child with refractory systemic juvenile idiopathic arthritis.
Authors: Morelle G; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France., Castelle M; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France., Pinto G; Pediatric Endocrinology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, Paris, France., Breton S; Pediatric Radiology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, Paris, France., Bendavid M; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France., Boussard C; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France., Mouy R; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France., Bader-Meunier B; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France.; Imagine Institute, Université de Paris, Paris, France.; Reference Center for Rheumatic, AutoImmune and Systemic diseases in children (RAISE), Paris, France.; Université de Paris, Paris, France., Semeraro M; Université de Paris, Paris, France.; Clinical Research Centre, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, Paris, France., Faye A; Université de Paris, Paris, France.; Pediatric Department, Robert Debre University Hospital, Assistance Publique Hôpitaux de Paris, Paris, France., Cavazzana M; Imagine Institute, Université de Paris, Paris, France.; Université de Paris, Paris, France.; Gene and Cellular Therapy Unit, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, Paris, France., Neven B; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France.; Imagine Institute, Université de Paris, Paris, France.; Université de Paris, Paris, France., Blanche S; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France.; Imagine Institute, Université de Paris, Paris, France.; Université de Paris, Paris, France., Quartier P; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France. pierre.quartier@aphp.fr.; Imagine Institute, Université de Paris, Paris, France. pierre.quartier@aphp.fr.; Reference Center for Rheumatic, AutoImmune and Systemic diseases in children (RAISE), Paris, France. pierre.quartier@aphp.fr.; Université de Paris, Paris, France. pierre.quartier@aphp.fr., Moshous D; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants-Malades University Hospital, Assistance Publique Hôpitaux de Paris, 149 rue de Sèvres, 75015, Paris, France.; Imagine Institute, Université de Paris, Paris, France.; Université de Paris, Paris, France.
Source: Pediatric rheumatology online journal [Pediatr Rheumatol Online J] 2021 Mar 12; Vol. 19 (1), pp. 27. Date of Electronic Publication: 2021 Mar 12.
Publication Type: Case Reports; Journal Article
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101248897 Publication Model: Electronic Cited Medium: Internet ISSN: 1546-0096 (Electronic) Linking ISSN: 15460096 NLM ISO Abbreviation: Pediatr Rheumatol Online J Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1546-0096
DOI:10.1186/s12969-021-00523-3