Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia.

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Bibliographic Details
Title: Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia.
Authors: Mueller A; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland., Paterson E; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA., McIntosh A; Novartis Development, Cambridge, Massachusetts, USA., Praestgaard J; Novartis Development, Cambridge, Massachusetts, USA., Bylo M; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA., Hoefling H; NIBR Informatics, Novartis Institute of Biomedical Research, Basel, Switzerland., Wells M; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA., Lynch DR; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA., Rummey C; Clinical Data Science GmbH, Basel, Switzerland., Krishnan ML; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland., Schultz M; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA., Malanga CJ; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
Source: Annals of clinical and translational neurology [Ann Clin Transl Neurol] 2021 Sep; Vol. 8 (9), pp. 1845-1856. Date of Electronic Publication: 2021 Aug 06.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Wiley Periodicals, Inc on behalf of American Neurological Association Country of Publication: United States NLM ID: 101623278 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2328-9503 (Electronic) Linking ISSN: 23289503 NLM ISO Abbreviation: Ann Clin Transl Neurol Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2328-9503
DOI:10.1002/acn3.51438