Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia.

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Title: Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia.
Authors: Mueller A; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland., Paterson E; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA., McIntosh A; Novartis Development, Cambridge, Massachusetts, USA., Praestgaard J; Novartis Development, Cambridge, Massachusetts, USA., Bylo M; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA., Hoefling H; NIBR Informatics, Novartis Institute of Biomedical Research, Basel, Switzerland., Wells M; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA., Lynch DR; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA., Rummey C; Clinical Data Science GmbH, Basel, Switzerland., Krishnan ML; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland., Schultz M; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA., Malanga CJ; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
Source: Annals of clinical and translational neurology [Ann Clin Transl Neurol] 2021 Sep; Vol. 8 (9), pp. 1845-1856. Date of Electronic Publication: 2021 Aug 06.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Wiley Periodicals, Inc on behalf of American Neurological Association Country of Publication: United States NLM ID: 101623278 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2328-9503 (Electronic) Linking ISSN: 23289503 NLM ISO Abbreviation: Ann Clin Transl Neurol Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia.
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  Data: <searchLink fieldCode="AU" term="%22Mueller+A%22">Mueller A</searchLink>; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Paterson+E%22">Paterson E</searchLink>; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22McIntosh+A%22">McIntosh A</searchLink>; Novartis Development, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Praestgaard+J%22">Praestgaard J</searchLink>; Novartis Development, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Bylo+M%22">Bylo M</searchLink>; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Hoefling+H%22">Hoefling H</searchLink>; NIBR Informatics, Novartis Institute of Biomedical Research, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Wells+M%22">Wells M</searchLink>; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Lynch+DR%22">Lynch DR</searchLink>; Division of Neurology, Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Rummey+C%22">Rummey C</searchLink>; Clinical Data Science GmbH, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Krishnan+ML%22">Krishnan ML</searchLink>; Translational Medicine, Novartis Institutes for BioMedical Research, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Schultz+M%22">Schultz M</searchLink>; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Malanga+CJ%22">Malanga CJ</searchLink>; Translational Medicine, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
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  Data: <searchLink fieldCode="JN" term="%22101623278%22">Annals of clinical and translational neurology</searchLink> [Ann Clin Transl Neurol] 2021 Sep; Vol. 8 (9), pp. 1845-1856. <i>Date of Electronic Publication: </i>2021 Aug 06.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Wiley+Periodicals%2C+Inc+on+behalf+of+American+Neurological+Association%22">Wiley Periodicals, Inc on behalf of American Neurological Association </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101623278 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2328-9503 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2223289503%22">23289503 </searchLink><i>NLM ISO Abbreviation: </i>Ann Clin Transl Neurol <i>Subsets: </i>MEDLINE
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