Progression to Loss of Ambulation Among Patients with Autosomal Recessive Limb-girdle Muscular Dystrophy: A Systematic Review.

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Bibliographic Details
Title: Progression to Loss of Ambulation Among Patients with Autosomal Recessive Limb-girdle Muscular Dystrophy: A Systematic Review.
Authors: Audhya IF; Sarepta Therapeutics Inc, Cambridge MA, USA., Cheung A; Broadstreet HEOR, Vancouver, BC, V6A 1A4 Canada., Szabo SM; Broadstreet HEOR, Vancouver, BC, V6A 1A4 Canada., Flint E; Broadstreet HEOR, Vancouver, BC, V6A 1A4 Canada., Weihl CC; Washington University School of Medicine, St. Louis, MO, USA., Gooch KL; Sarepta Therapeutics Inc, Cambridge MA, USA.
Source: Journal of neuromuscular diseases [J Neuromuscul Dis] 2022; Vol. 9 (4), pp. 477-492.
Publication Type: Systematic Review; Journal Article
Journal Info: Publisher: SAGE Publications Country of Publication: United States NLM ID: 101649948 Publication Model: Print Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:2214-3602
DOI:10.3233/JND-210771