Progression to Loss of Ambulation Among Patients with Autosomal Recessive Limb-girdle Muscular Dystrophy: A Systematic Review.
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| Title: | Progression to Loss of Ambulation Among Patients with Autosomal Recessive Limb-girdle Muscular Dystrophy: A Systematic Review. |
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| Authors: | Audhya IF; Sarepta Therapeutics Inc, Cambridge MA, USA., Cheung A; Broadstreet HEOR, Vancouver, BC, V6A 1A4 Canada., Szabo SM; Broadstreet HEOR, Vancouver, BC, V6A 1A4 Canada., Flint E; Broadstreet HEOR, Vancouver, BC, V6A 1A4 Canada., Weihl CC; Washington University School of Medicine, St. Louis, MO, USA., Gooch KL; Sarepta Therapeutics Inc, Cambridge MA, USA. |
| Source: | Journal of neuromuscular diseases [J Neuromuscul Dis] 2022; Vol. 9 (4), pp. 477-492. |
| Publication Type: | Systematic Review; Journal Article |
| Journal Info: | Publisher: SAGE Publications Country of Publication: United States NLM ID: 101649948 Publication Model: Print Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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