Translational potential of base-editing tools for gene therapy of monogenic diseases.

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Bibliographic Details
Title: Translational potential of base-editing tools for gene therapy of monogenic diseases.
Authors: Reshetnikov VV; Department of Biotechnology, Sirius University of Science and Technology, Sochi, Russia.; Department of Molecular Genetics, Institute of Cytology and Genetics, Novosibirsk, Russia., Chirinskaite AV; Сenter of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia., Sopova JV; Сenter of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.; Laboratory of Amyloid Biology, St. Petersburg State University, St. Petersburg, Russia., Ivanov RA; Department of Biotechnology, Sirius University of Science and Technology, Sochi, Russia., Leonova EI; Сenter of Transgenesis and Genome Editing, St. Petersburg State University, St. Petersburg, Russia.; Scientific Center for Genetics and Life Sciences, Sirius University of Science and Technology, Sochi, Russia.
Source: Frontiers in bioengineering and biotechnology [Front Bioeng Biotechnol] 2022 Aug 10; Vol. 10, pp. 942440. Date of Electronic Publication: 2022 Aug 10 (Print Publication: 2022).
Publication Type: Journal Article; Review
Journal Info: Publisher: Frontiers Media S.A Country of Publication: Switzerland NLM ID: 101632513 Publication Model: eCollection Cited Medium: Print ISSN: 2296-4185 (Print) Linking ISSN: 22964185 NLM ISO Abbreviation: Front Bioeng Biotechnol Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2296-4185
DOI:10.3389/fbioe.2022.942440