| Authors: |
Johnson TB; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States.; Amicus Therapeutics, Cranbury, NJ, United States., Brudvig JJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States.; Amicus Therapeutics, Cranbury, NJ, United States., Likhite S; The Research Institute at Nationwide Children's Hospital, Columbus, OH, United States., Pratt MA; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States., White KA; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States., Cain JT; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States.; Amicus Therapeutics, Cranbury, NJ, United States., Booth CD; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States., Timm DJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States., Davis SS; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States., Meyerink B; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States., Pineda R; The Research Institute at Nationwide Children's Hospital, Columbus, OH, United States., Dennys-Rivers C; The Research Institute at Nationwide Children's Hospital, Columbus, OH, United States., Kaspar BK; The Research Institute at Nationwide Children's Hospital, Columbus, OH, United States., Meyer K; The Research Institute at Nationwide Children's Hospital, Columbus, OH, United States., Weimer JM; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, United States.; Amicus Therapeutics, Cranbury, NJ, United States.; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Vermillion, SD, United States. |