Outcomes of 38 patients with PFIC3: Impact of genotype and of response to ursodeoxycholic acid therapy.

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Title: Outcomes of 38 patients with PFIC3: Impact of genotype and of response to ursodeoxycholic acid therapy.
Authors: Gonzales E; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Gardin A; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Almes M; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Darmellah-Remil A; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France., Seguin H; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France., Mussini C; Pathology, Bicêtre Hospital, Assistance Publique - Hôpitaux de Paris, University Paris-Saclay, Le Kremlin-Bicêtre, France., Franchi-Abella S; Pediatric Radiology, Bicêtre Hospital, Assistance Publique - Hôpitaux de Paris, University Paris-Saclay, Le Kremlin-Bicêtre, France., Duché M; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Pediatric Radiology, Bicêtre Hospital, Assistance Publique - Hôpitaux de Paris, University Paris-Saclay, Le Kremlin-Bicêtre, France., Ackermann O; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Thébaut A; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Habes D; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Hermeziu B; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Lapalus M; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Falguières T; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Combal JP; Vivet Therapeutics, Paris, France., Benichou B; Vivet Therapeutics, Paris, France., Valero S; Vivet Therapeutics, Paris, France., Davit-Spraul A; Biochemistry; Bicêtre Hospital, Assistance Publique - Hôpitaux de Paris, University Paris-Saclay, Le Kremlin-Bicêtre, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France., Jacquemin E; Pediatric Hepatology and Liver Transplantation, National Reference Centre for Biliary Atresia and Genetic Cholestasis, FILFOIE, ERN RARE LIVER, France.; Inserm U1193, Hepatinov, University Paris-Saclay, Orsay, France.
Source: JHEP reports : innovation in hepatology [JHEP Rep] 2023 Jul 13; Vol. 5 (10), pp. 100844. Date of Electronic Publication: 2023 Jul 13 (Print Publication: 2023).
Publication Type: Journal Article
Journal Info: Publisher: Elsevier B.V Country of Publication: Netherlands NLM ID: 101761237 Publication Model: eCollection Cited Medium: Internet ISSN: 2589-5559 (Electronic) Linking ISSN: 25895559 NLM ISO Abbreviation: JHEP Rep Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2589-5559
DOI:10.1016/j.jhepr.2023.100844