| Authors: |
Byrne BJ; Department of Pediatrics in the College of Medicine, University of Florida, Gainesville, FL, United States., Parenti G; Metabolic Unit, Department of Translational Medical Sciences, University of Naples Federico II, Naples, Italy.; Telethon Institute of Genetics and Medicine, Pozzuoli, Italy., Schoser B; Friedrich-Baur-Institute, Department of Neurology, LMU University Hospital, LMU Munich, Munich, Germany., van der Ploeg AT; Erasmus MC University Medical Center, Rotterdam, Netherlands., Do H; M6P-Therapeutics, St Louis, MO, United States., Fox B; Amicus Therapeutics, Inc., Princeton, NJ, United States., Goldman M; Amicus Therapeutics, Inc., Princeton, NJ, United States., Johnson FK; Amicus Therapeutics, Inc., Princeton, NJ, United States., Kang J; Metrum Research Group, Tariffville, CT, United States., Mehta N; Amicus Therapeutics, Inc., Princeton, NJ, United States., Mondick J; Incyte Corporation, Wilmington, DE, United States., Sheikh MO; Amicus Therapeutics, Inc., Princeton, NJ, United States., Sitaraman Das S; Amicus Therapeutics, Inc., Princeton, NJ, United States., Tuske S; Amicus Therapeutics, Inc., Princeton, NJ, United States., Brudvig J; Amicus Therapeutics, Inc., Princeton, NJ, United States., Weimer JM; Amicus Therapeutics, Inc., Princeton, NJ, United States., Mozaffar T; Department of Neurology, University of California, Irvine, Irvine, CA, United States. |