Identification of small molecule agonists of fetal hemoglobin expression for the treatment of sickle cell disease.

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Title: Identification of small molecule agonists of fetal hemoglobin expression for the treatment of sickle cell disease.
Authors: Yang JP; Takeda Development Center Americas, Inc., San Diego, California, United States of America., Toughiri R; Takeda Development Center Americas, Inc., San Diego, California, United States of America., Gounder AP; Takeda Development Center Americas, Inc., San Diego, California, United States of America., Scheibe D; Takeda Development Center Americas, Inc., San Diego, California, United States of America., Petrus M; Takeda Development Center Americas, Inc., San Diego, California, United States of America., Fink SJ; Takeda Development Center Americas, Inc., Cambridge, Massachusetts, United States of America., Vallee S; Takeda Development Center Americas, Inc., Cambridge, Massachusetts, United States of America., Kenniston J; Takeda Development Center Americas, Inc., Cambridge, Massachusetts, United States of America., Papaioannou N; Takeda Development Center Americas, Inc., Cambridge, Massachusetts, United States of America., Langston S; Takeda Development Center Americas, Inc., Cambridge, Massachusetts, United States of America., Gavva NR; Takeda Development Center Americas, Inc., San Diego, California, United States of America., Horman SR; Takeda Development Center Americas, Inc., San Diego, California, United States of America.
Source: PloS one [PLoS One] 2024 Nov 06; Vol. 19 (11), pp. e0307049. Date of Electronic Publication: 2024 Nov 06 (Print Publication: 2024).
Publication Type: Journal Article
Journal Info: Publisher: Public Library of Science Country of Publication: United States NLM ID: 101285081 Publication Model: eCollection Cited Medium: Internet ISSN: 1932-6203 (Electronic) Linking ISSN: 19326203 NLM ISO Abbreviation: PLoS One Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1932-6203
DOI:10.1371/journal.pone.0307049