Systematic literature review of the impact of spinal muscular atrophy therapies on bulbar function.
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| Title: | Systematic literature review of the impact of spinal muscular atrophy therapies on bulbar function. |
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| Authors: | McGrattan K; Department of Speech-Language-Hearing Sciences, University of Minnesota, Minneapolis, MN, USA., Walsh K; Department of Rehabilitation, Lurie Children's Hospital, Chicago, IL, USA., Mehl L; Biomedical Research, Novartis, Cambridge, MA, USA., Kaur S; Novartis, Madhapur / Hyderabad, India., Dilly KW; Novartis Gene Therapies, Inc., Bannockburn, IL, USA. |
| Source: | Journal of neuromuscular diseases [J Neuromuscul Dis] 2025 Mar; Vol. 12 (2), pp. 195-217. Date of Electronic Publication: 2024 Dec 20. |
| Publication Type: | Journal Article; Systematic Review |
| Journal Info: | Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 2214-3602 |
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| DOI: | 10.1177/22143602241303373 |