AAV9-mediated MYBPC3 gene therapy with optimized expression cassette enhances cardiac function and survival in MYBPC3 cardiomyopathy models.

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Bibliographic Details
Title: AAV9-mediated MYBPC3 gene therapy with optimized expression cassette enhances cardiac function and survival in MYBPC3 cardiomyopathy models.
Authors: Greer-Short A; Tenaya Therapeutics, South San Francisco, CA, USA., Greenwood A; Tenaya Therapeutics, South San Francisco, CA, USA., Leon EC; Tenaya Therapeutics, South San Francisco, CA, USA., Qureshi TN; Tenaya Therapeutics, South San Francisco, CA, USA., von Kraut K; Tenaya Therapeutics, South San Francisco, CA, USA., Wong J; Tenaya Therapeutics, South San Francisco, CA, USA., Tsui JH; Tenaya Therapeutics, South San Francisco, CA, USA., Reid CA; Tenaya Therapeutics, South San Francisco, CA, USA., Cheng Z; Tenaya Therapeutics, South San Francisco, CA, USA., Easter E; Tenaya Therapeutics, South San Francisco, CA, USA., Yang J; Tenaya Therapeutics, South San Francisco, CA, USA., Ho J; Tenaya Therapeutics, South San Francisco, CA, USA., Steltzer S; Tenaya Therapeutics, South San Francisco, CA, USA., Budan A; Tenaya Therapeutics, South San Francisco, CA, USA., Cho M; Tenaya Therapeutics, South San Francisco, CA, USA., Chandrakumar R; Tenaya Therapeutics, South San Francisco, CA, USA., Cisne-Thompson O; Tenaya Therapeutics, South San Francisco, CA, USA., Feathers C; Tenaya Therapeutics, South San Francisco, CA, USA., Chung TW; Tenaya Therapeutics, South San Francisco, CA, USA., Rodriguez N; Tenaya Therapeutics, South San Francisco, CA, USA., Jones S; Tenaya Therapeutics, South San Francisco, CA, USA., Alleyne-Levy C; Tenaya Therapeutics, South San Francisco, CA, USA., Liu J; Tenaya Therapeutics, South San Francisco, CA, USA., Jing F; Tenaya Therapeutics, South San Francisco, CA, USA., Prince WS; Tenaya Therapeutics, South San Francisco, CA, USA., Lin J; Tenaya Therapeutics, South San Francisco, CA, USA., Ivey KN; Tenaya Therapeutics, South San Francisco, CA, USA., Tingley WG; Tenaya Therapeutics, South San Francisco, CA, USA., Hoey T; Tenaya Therapeutics, South San Francisco, CA, USA., Lombardi LM; Tenaya Therapeutics, South San Francisco, CA, USA. llombardi@tenayathera.com.
Source: Nature communications [Nat Commun] 2025 Mar 04; Vol. 16 (1), pp. 2196. Date of Electronic Publication: 2025 Mar 04.
Publication Type: Journal Article
Journal Info: Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2041-1723
DOI:10.1038/s41467-025-57481-7