Long-term safety and effectiveness of fenfluramine in children and adults with Dravet syndrome.

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Title: Long-term safety and effectiveness of fenfluramine in children and adults with Dravet syndrome.
Authors: Scheffer IE; Austin Hospital and Royal Children's Hospital, Florey and Murdoch Children's Research Institutes, University of Melbourne, Melbourne, Victoria, Australia., Nabbout R; Member of the European Reference Network EpiCARE, Reference Centre for Rare Epilepsies, Necker Enfants Malades Hospital, APHP, Institut Imagine, INSERM U1163, Université Paris Cité, Paris, France., Lagae L; Member of the European Reference Network EpiCARE, University of Leuven, Leuven, Belgium., Devinsky O; NYU Langone Medical Center, New York City, New York, USA., Auvin S; Member of the European Reference Network EpiCARE, APHP, Centre de Référence Epilepsies Rares, Hôpital Universitaire Robert-Debré, Paris, France.; Université Paris-Cité, INSERM Neuro Diderot, Paris, France.; Institut Universitaire de France (IUF), Paris, France., Thiele EA; Massachusetts General Hospital, Boston, Massachusetts, USA., Wirrell EC; Mayo Clinic, Rochester, Minnesota, USA., Polster T; Krankenhaus Mara-Bethel Epilepsy Centre, Medical School OWL, Bielefeld University, Bielefeld, Germany., Specchio N; Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.; Member of the European Reference Network EpiCARE, University Hospitals KU, Leuven, Belgium., Pringsheim M; Schön Klinik Vogtareuth, Vogtareuth, Germany.; PMU Salzburg, Salzburg, Austria.; German Heart Centre, TUM, Munich, Germany., Imai K; NHO Shizuoka Institute of Epilepsy and Neurological Disorders, Shizuoka, Japan., Lock MD; Independent Statistical Consultant, Haiku, Hawaii, USA., Langlois M; UCB, Colombes, France., Roper RZ; UCB, Slough, UK., Lothe A; UCB, Colombes, France., Sullivan J; University of California San Francisco Weill Institute for Neurosciences, Benioff Children's Hospital, San Francisco, California, USA.
Source: Epilepsia [Epilepsia] 2025 Jun; Vol. 66 (6), pp. 1919-1932. Date of Electronic Publication: 2025 Mar 12.
Publication Type: Journal Article; Randomized Controlled Trial
Journal Info: Publisher: Blackwell Science Country of Publication: United States NLM ID: 2983306R Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-1167 (Electronic) Linking ISSN: 00139580 NLM ISO Abbreviation: Epilepsia Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1528-1167
DOI:10.1111/epi.18342