Preclinical development of genome editing to treat Duchenne muscular dystrophy by exon skipping.

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Bibliographic Details
Title: Preclinical development of genome editing to treat Duchenne muscular dystrophy by exon skipping.
Authors: Padmaswari MH; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.; Cell and Molecular Biology, University of Arkansas, Fayetteville, AR, USA., Agrawal S; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA., Nelson CE; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.; Cell and Molecular Biology, University of Arkansas, Fayetteville, AR, USA.
Source: Journal of neuromuscular diseases [J Neuromuscul Dis] 2025 May; Vol. 12 (3), pp. 424-434. Date of Electronic Publication: 2025 Mar 19.
Publication Type: Journal Article; Review
Journal Info: Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:2214-3602
DOI:10.1177/22143602251326993