Preclinical development of genome editing to treat Duchenne muscular dystrophy by exon skipping.
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| Title: | Preclinical development of genome editing to treat Duchenne muscular dystrophy by exon skipping. |
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| Authors: | Padmaswari MH; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.; Cell and Molecular Biology, University of Arkansas, Fayetteville, AR, USA., Agrawal S; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA., Nelson CE; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.; Cell and Molecular Biology, University of Arkansas, Fayetteville, AR, USA. |
| Source: | Journal of neuromuscular diseases [J Neuromuscul Dis] 2025 May; Vol. 12 (3), pp. 424-434. Date of Electronic Publication: 2025 Mar 19. |
| Publication Type: | Journal Article; Review |
| Journal Info: | Publisher: IOS Press Country of Publication: United States NLM ID: 101649948 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 40105473 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Preclinical development of genome editing to treat Duchenne muscular dystrophy by exon skipping. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Padmaswari+MH%22">Padmaswari MH</searchLink>; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.; Cell and Molecular Biology, University of Arkansas, Fayetteville, AR, USA.<br /><searchLink fieldCode="AU" term="%22Agrawal+S%22">Agrawal S</searchLink>; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.<br /><searchLink fieldCode="AU" term="%22Nelson+CE%22">Nelson CE</searchLink>; Biomedical Engineering, University of Arkansas, Fayetteville, AR, USA.; Cell and Molecular Biology, University of Arkansas, Fayetteville, AR, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101649948%22">Journal of neuromuscular diseases</searchLink> [J Neuromuscul Dis] 2025 May; Vol. 12 (3), pp. 424-434. <i>Date of Electronic Publication: </i>2025 Mar 19. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Review – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22IOS+Press%22">IOS Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101649948 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2214-3602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222143599%22">22143599 </searchLink><i>NLM ISO Abbreviation: </i>J Neuromuscul Dis <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=40105473 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1177/22143602251326993 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 424 Titles: – TitleFull: Preclinical development of genome editing to treat Duchenne muscular dystrophy by exon skipping. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Padmaswari MH – PersonEntity: Name: NameFull: Agrawal S – PersonEntity: Name: NameFull: Nelson CE IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 05 Text: 2025 May Type: published Y: 2025 Identifiers: – Type: issn-electronic Value: 2214-3602 Numbering: – Type: volume Value: 12 – Type: issue Value: 3 Titles: – TitleFull: Journal of neuromuscular diseases Type: main |
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