Effect of creatine monohydrate on motor function in children with facioscapulohumeral muscular dystrophy: A multicenter, randomized, double-blind placebo-controlled crossover trial.

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Title: Effect of creatine monohydrate on motor function in children with facioscapulohumeral muscular dystrophy: A multicenter, randomized, double-blind placebo-controlled crossover trial.
Authors: Woodcock IR; Department of Neurology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Victoria, Australia., de Valle K; Department of Neurology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia.; Department of Physiotherapy, University of Melbourne, Melbourne, Victoria, Australia., Cairns A; Neurosciences Department, Queensland Children's Hospital, Brisbane, Queensland, Australia., Davidson ZE; Department of Neurology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia.; Department of Nutrition, Dietetics and Food, Monash University, Melbourne, Victoria, Australia., Kean M; Department of Medical Imaging, The Royal Children's Hospital, Melbourne, Victoria, Australia., Varma N; Department of Medical Imaging, The Royal Children's Hospital, Melbourne, Victoria, Australia., Grobler A; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Victoria, Australia., Metz D; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia.; Department of Nephrology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; Department of Paediatrics, Monash University, Melbourne, Victoria, Australia., Carroll K; Department of Neurology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia., Dilek N; Center for Health and Technology, University of Rochester, Rochester, New York, USA., Heatwole C; Center for Health and Technology, University of Rochester, Rochester, New York, USA., Ryan MM; Department of Neurology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia., Delatycki MB; Department of Paediatrics, University of Melbourne, Melbourne, Victoria, Australia.; Victorian Clinical Genetics Service, Melbourne, Victoria, Australia.; Bruce Lefroy Centre for Genetic Research, Murdoch Children's Research Institute, Melbourne, Victoria, Australia., Yiu EM; Department of Neurology, The Royal Children's Hospital, Melbourne, Victoria, Australia.; The Murdoch Children's Research Institute, Melbourne, Victoria, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Victoria, Australia.
Source: Pharmacotherapy [Pharmacotherapy] 2025 Jun; Vol. 45 (6), pp. 341-351. Date of Electronic Publication: 2025 May 14.
Publication Type: Journal Article; Randomized Controlled Trial; Multicenter Study
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 8111305 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1875-9114 (Electronic) Linking ISSN: 02770008 NLM ISO Abbreviation: Pharmacotherapy Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1875-9114
DOI:10.1002/phar.70025