Phase 1 study of ABI-009 (nab-rapamycin) for surgically refractory epilepsy (RaSuRE).

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Bibliographic Details
Title: Phase 1 study of ABI-009 (nab-rapamycin) for surgically refractory epilepsy (RaSuRE).
Authors: Hall K; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA.; Department of Epidemiology, Johns Hopkins Bloomberg School of Public Health, Baltimore, Maryland, USA., Saneto R; Department of Neurology, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Randle S; Department of Neurology, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Wainwright MS; Department of Neurology, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Berry P; Department of Neurology, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Leary S; Cancer and Blood Disorders Center, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Mirzaa G; Department of Genetic Medicine, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Lockrow J; Department of Neurology, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Goldstein H; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Ojemann J; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Thiessen R; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Willis H; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Sullivan E; Biostats, Epidemiology, and Analytics in Research Core, Seattle Children's Hospital, Seattle, Washington, USA., Rivers R; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Klein J; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA., Hauptman JS; Division of Neurosurgery, Department of Neurological Surgery, Seattle Children's Hospital, University of Washington, Seattle, Washington, USA.; Division of Neurosurgery, Barrow Neurological Institute, Phoenix Children's Hospital, Phoenix, Arizona, USA.
Source: Epilepsia [Epilepsia] 2025 Nov; Vol. 66 (11), pp. 4246-4258. Date of Electronic Publication: 2025 Jul 19.
Publication Type: Journal Article; Clinical Trial, Phase I
Journal Info: Publisher: Blackwell Science Country of Publication: United States NLM ID: 2983306R Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-1167 (Electronic) Linking ISSN: 00139580 NLM ISO Abbreviation: Epilepsia Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1528-1167
DOI:10.1111/epi.18555