Lysosomal polyamine storage upon ATP13A2 loss impairs β-glucocerebrosidase via altered lysosomal pH and electrostatic hydrolase-lipid interactions.

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Title: Lysosomal polyamine storage upon ATP13A2 loss impairs β-glucocerebrosidase via altered lysosomal pH and electrostatic hydrolase-lipid interactions.
Authors: Samaddar M; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Fitzgerald GA; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Nguyen AH; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Davis SS; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Jain S; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Guo J; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Propson NE; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., van Lengerich B; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Shi Y; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Balasundar S; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Rougé L; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Alkabsh J; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Rana A; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Yi J; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Chin MY; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Becerra IA; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Arguello A; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Fox BM; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Logan T; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Suh JH; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Henry AG; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA., Di Paolo G; Denali Therapeutics, Inc., South San Francisco, CA 94080, USA. Electronic address: dipaolo@dnli.com.
Source: Cell reports [Cell Rep] 2025 Sep 23; Vol. 44 (9), pp. 116179. Date of Electronic Publication: 2025 Aug 22.
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101573691 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2211-1247 (Electronic) NLM ISO Abbreviation: Cell Rep Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2211-1247
DOI:10.1016/j.celrep.2025.116179