Generalizable features of pegRNA design for prime editing of inherited retinal diseases.

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Bibliographic Details
Title: Generalizable features of pegRNA design for prime editing of inherited retinal diseases.
Authors: Patterson FM; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Nguyen Tran MT; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Department of Chemistry, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA., Guinan T; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Mohd Khalid MKN; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Kc R; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Fairfax KA; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Liu GS; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; Ophthalmology, Department of Surgery, University of Melbourne, Victoria, Australia., Cook AL; Wicking Dementia Research and Education Centre, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Hung SS; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; Ophthalmology, Department of Surgery, University of Melbourne, Victoria, Australia., Hewitt AW; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; School of Medicine, College of Health and Medicine, University of Tasmania, Tasmania, Australia.
Source: Ophthalmic genetics [Ophthalmic Genet] 2026 Feb; Vol. 47 (1), pp. 59-66. Date of Electronic Publication: 2025 Nov 09.
Publication Type: Journal Article
Journal Info: Publisher: Informa Healthcare Country of Publication: England NLM ID: 9436057 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1744-5094 (Electronic) Linking ISSN: 13816810 NLM ISO Abbreviation: Ophthalmic Genet Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1744-5094
DOI:10.1080/13816810.2025.2576786