Generalizable features of pegRNA design for prime editing of inherited retinal diseases.

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Title: Generalizable features of pegRNA design for prime editing of inherited retinal diseases.
Authors: Patterson FM; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Nguyen Tran MT; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Department of Chemistry, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA., Guinan T; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Mohd Khalid MKN; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Kc R; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Fairfax KA; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Liu GS; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; Ophthalmology, Department of Surgery, University of Melbourne, Victoria, Australia., Cook AL; Wicking Dementia Research and Education Centre, College of Health and Medicine, University of Tasmania, Tasmania, Australia., Hung SS; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; Ophthalmology, Department of Surgery, University of Melbourne, Victoria, Australia., Hewitt AW; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; School of Medicine, College of Health and Medicine, University of Tasmania, Tasmania, Australia.
Source: Ophthalmic genetics [Ophthalmic Genet] 2026 Feb; Vol. 47 (1), pp. 59-66. Date of Electronic Publication: 2025 Nov 09.
Publication Type: Journal Article
Journal Info: Publisher: Informa Healthcare Country of Publication: England NLM ID: 9436057 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1744-5094 (Electronic) Linking ISSN: 13816810 NLM ISO Abbreviation: Ophthalmic Genet Subsets: MEDLINE
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  Data: Generalizable features of pegRNA design for prime editing of inherited retinal diseases.
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  Data: <searchLink fieldCode="AU" term="%22Patterson+FM%22">Patterson FM</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.<br /><searchLink fieldCode="AU" term="%22Nguyen+Tran+MT%22">Nguyen Tran MT</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Department of Chemistry, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Guinan+T%22">Guinan T</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.<br /><searchLink fieldCode="AU" term="%22Mohd+Khalid+MKN%22">Mohd Khalid MKN</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.<br /><searchLink fieldCode="AU" term="%22Kc+R%22">Kc R</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.<br /><searchLink fieldCode="AU" term="%22Fairfax+KA%22">Fairfax KA</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.<br /><searchLink fieldCode="AU" term="%22Liu+GS%22">Liu GS</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; Ophthalmology, Department of Surgery, University of Melbourne, Victoria, Australia.<br /><searchLink fieldCode="AU" term="%22Cook+AL%22">Cook AL</searchLink>; Wicking Dementia Research and Education Centre, College of Health and Medicine, University of Tasmania, Tasmania, Australia.<br /><searchLink fieldCode="AU" term="%22Hung+SS%22">Hung SS</searchLink>; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; Ophthalmology, Department of Surgery, University of Melbourne, Victoria, Australia.<br /><searchLink fieldCode="AU" term="%22Hewitt+AW%22">Hewitt AW</searchLink>; Menzies Institute for Medical Research, College of Health and Medicine, University of Tasmania, Tasmania, Australia.; Centre for Eye Research Australia, University of Melbourne, Victoria, Australia.; School of Medicine, College of Health and Medicine, University of Tasmania, Tasmania, Australia.
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  Data: <searchLink fieldCode="JN" term="%229436057%22">Ophthalmic genetics</searchLink> [Ophthalmic Genet] 2026 Feb; Vol. 47 (1), pp. 59-66. <i>Date of Electronic Publication: </i>2025 Nov 09.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Informa+Healthcare%22">Informa Healthcare </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9436057 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1744-5094 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2213816810%22">13816810 </searchLink><i>NLM ISO Abbreviation: </i>Ophthalmic Genet <i>Subsets: </i>MEDLINE
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        Value: 10.1080/13816810.2025.2576786
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      – Code: eng
        Text: English
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              Text: 2026 Feb
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              Y: 2026
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